{"id":85134,"date":"2026-01-05T22:10:39","date_gmt":"2026-01-05T13:10:39","guid":{"rendered":"https:\/\/www.marketresearch.co.jp\/insights\/enzyme-replacement-therapy-mordor\/"},"modified":"2026-04-03T15:38:17","modified_gmt":"2026-04-03T06:38:17","slug":"enzyme-replacement-therapy-mordor","status":"publish","type":"post","link":"https:\/\/www.marketresearch.co.jp\/insights\/enzyme-replacement-therapy-mordor\/","title":{"rendered":"\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u5e02\u5834\uff1a\u898f\u6a21\u30fb\u30b7\u30a7\u30a2\u5206\u6790\u3001\u6210\u9577\u30c8\u30ec\u30f3\u30c9\u3068\u4e88\u6e2c (2025-2030\u5e74)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.marketresearch.co.jp\/insights\/wp-content\/uploads\/2026\/01\/enzyme-replacement-therapy-1750345040349-major-players.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.marketresearch.co.jp\/insights\/wp-content\/uploads\/2026\/01\/enzyme-replacement-therapy-size-image-1750344801180.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">\n    1. \u306f\u3058\u3081\u306b<\/p>\n<ul>\n<li class=\"toc-level-2\">\n          1.1 \u8abf\u67fb\u306e\u524d\u63d0\u3068\u5e02\u5834\u306e\u5b9a\u7fa9<\/p>\n<\/li>\n<li class=\"toc-level-2\">\n          1.2 \u8abf\u67fb\u7bc4\u56f2<\/p>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">\n    2. \u8abf\u67fb\u65b9\u6cd5<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">\n    3. \u30a8\u30b0\u30bc\u30af\u30c6\u30a3\u30d6\u30b5\u30de\u30ea\u30fc<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">\n    4. \u5e02\u5834\u6982\u6cc1<\/p>\n<ul>\n<li class=\"toc-level-2\">\n          4.1 \u5e02\u5834\u6982\u8981<\/p>\n<\/li>\n<li class=\"toc-level-2\">\n          4.2 \u5e02\u5834\u306e\u63a8\u9032\u8981\u56e0<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          4.2.1 \u5e0c\u5c11\u75be\u60a3\u306e\u6709\u75c5\u7387\u306e\u5897\u52a0<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.2.2 \u653f\u5e9c\u306e\u30a4\u30f3\u30bb\u30f3\u30c6\u30a3\u30d6\u3068\u8cc7\u91d1\u63d0\u4f9b<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.2.3 \u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u30d7\u30ed\u30b0\u30e9\u30e0\u306e\u62e1\u5927<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.2.4 \u60a3\u8005\u4e2d\u5fc3\u306e\u63d0\u4f9b\u3078\u306e\u79fb\u884c<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.2.5 \u9175\u7d20\u5de5\u5b66\u306b\u304a\u3051\u308b\u6280\u8853\u7684\u9032\u6b69<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.2.6 \u9769\u65b0\u7684\u306a\u511f\u9084\u30e2\u30c7\u30eb<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">\n          4.3 \u5e02\u5834\u306e\u963b\u5bb3\u8981\u56e0<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          4.3.1 \u9ad8\u984d\u306a\u6cbb\u7642\u8cbb<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.3.2 \u514d\u75ab\u539f\u6027\u306e\u61f8\u5ff5<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.3.3 \u65b0\u8208\u6cbb\u7642\u6cd5\u3068\u306e\u7af6\u5408<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.3.4 \u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u306e\u8ab2\u984c<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">\n          4.4 \u898f\u5236\u74b0\u5883<\/p>\n<\/li>\n<li class=\"toc-level-2\">\n          4.5 \u30dd\u30fc\u30bf\u30fc\u306e5\u3064\u306e\u529b\u5206\u6790<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          4.5.1 \u65b0\u898f\u53c2\u5165\u8005\u306e\u8105\u5a01<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.5.2 \u8cb7\u3044\u624b\u306e\u4ea4\u6e09\u529b<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.5.3 \u4f9b\u7d66\u8005\u306e\u4ea4\u6e09\u529b<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.5.4 \u4ee3\u66ff\u54c1\u306e\u8105\u5a01<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          4.5.5 \u7af6\u4e89\u4e0a\u306e\u5bfe\u7acb<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">\n    5. \u5e02\u5834\u898f\u6a21\u3068\u6210\u9577\u4e88\u6e2c (\u91d1\u984d\u3001\u7c73\u30c9\u30eb)<\/p>\n<ul>\n<li class=\"toc-level-2\">\n          5.1 \u9175\u7d20\u30bf\u30a4\u30d7\u5225<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          5.1.1 \u30a4\u30df\u30b0\u30eb\u30bb\u30e9\u30fc\u30bc<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.1.2 \u30a2\u30ac\u30eb\u30b7\u30c0\u30fc\u30bc \u30a2\u30eb\u30d5\u30a1<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.1.3 \u30a2\u30ac\u30eb\u30b7\u30c0\u30fc\u30bc \u30d9\u30fc\u30bf<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.1.4 \u30d9\u30e9\u30b0\u30eb\u30bb\u30e9\u30fc\u30bc \u30a2\u30eb\u30d5\u30a1<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.1.5 \u30bf\u30ea\u30b0\u30eb\u30bb\u30e9\u30fc\u30bc \u30a2\u30eb\u30d5\u30a1<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.1.6 \u30a2\u30eb\u30b0\u30eb\u30b3\u30b7\u30c0\u30fc\u30bc \u30a2\u30eb\u30d5\u30a1<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.1.7 \u30a2\u30d0\u30eb\u30b0\u30eb\u30b3\u30b7\u30c0\u30fc\u30bc \u30a2\u30eb\u30d5\u30a1<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.1.8 \u30ac\u30eb\u30b9\u30eb\u30d5\u30a1\u30fc\u30bc<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.1.9 \u30a4\u30c9\u30a5\u30eb\u30b9\u30eb\u30d5\u30a1\u30fc\u30bc<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.1.10 \u305d\u306e\u4ed6\u306e\u9175\u7d20<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">\n          5.2 \u7528\u9014\u5225<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          5.2.1 \u30b4\u30fc\u30b7\u30a7\u75c5\uff08I\u578b\u3001II\u578b\u3001III\u578b\uff09<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.2.2 \u30dd\u30f3\u30da\u75c5\uff08\u4e73\u5150\u578b &amp; \u9045\u767a\u578b\uff09<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.2.3 \u30d5\u30a1\u30d6\u30ea\u30fc\u75c5<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.2.4 MPS I\uff08\u30cf\u30fc\u30e9\u30fc\u75c7\u5019\u7fa4\uff09<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.2.5 MPS II\uff08\u30cf\u30f3\u30bf\u30fc\u75c7\u5019\u7fa4\uff09<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.2.6 MPS IV\uff08\u30e2\u30eb\u30ad\u30aa\u75c7\u5019\u7fa4\uff09<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.2.7 \u305d\u306e\u4ed6\u306e\u7528\u9014<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">\n          5.3 \u6295\u4e0e\u7d4c\u8def\u5225<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          5.3.1 \u9759\u8108\u5185\u6ce8\u5165<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.3.2 \u76ae\u4e0b<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">\n          5.4 \u88fd\u5264\u5225<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          5.4.1 \u6a19\u6e96\u7d44\u63db\u3048\u9175\u7d20<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.4.2 PEG\u5316 \/ \u878d\u5408\u30bf\u30f3\u30d1\u30af\u8cea<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.4.3 \u907a\u4f1d\u5b50\u6d3b\u6027\u5316\u6b21\u4e16\u4ee3\u9175\u7d20<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">\n          5.5 \u30a8\u30f3\u30c9\u30e6\u30fc\u30b6\u30fc\u5225<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          5.5.1 \u75c5\u9662 &amp; \u5c02\u9580\u30af\u30ea\u30cb\u30c3\u30af<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.5.2 \u5728\u5b85\u533b\u7642\u65bd\u8a2d<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.5.3 \u6ce8\u5165\u30bb\u30f3\u30bf\u30fc<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">\n          5.6 \u5730\u57df\u5225<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          5.6.1 \u5317\u7c73<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.1.1 \u7c73\u56fd<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.1.2 \u30ab\u30ca\u30c0<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.1.3 \u30e1\u30ad\u30b7\u30b3<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.6.2 \u6b27\u5dde<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.2.1 \u30c9\u30a4\u30c4<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.2.2 \u82f1\u56fd<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.2.3 \u30d5\u30e9\u30f3\u30b9<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.2.4 \u30a4\u30bf\u30ea\u30a2<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.2.5 \u30b9\u30da\u30a4\u30f3<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.2.6 \u305d\u306e\u4ed6\u306e\u6b27\u5dde<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.6.3 \u30a2\u30b8\u30a2\u592a\u5e73\u6d0b<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.3.1 \u4e2d\u56fd<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.3.2 \u65e5\u672c<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.3.3 \u30a4\u30f3\u30c9<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.3.4 \u30aa\u30fc\u30b9\u30c8\u30e9\u30ea\u30a2<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.3.5 \u97d3\u56fd<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.3.6 \u305d\u306e\u4ed6\u306e\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.6.4 \u4e2d\u6771 &amp; \u30a2\u30d5\u30ea\u30ab<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.4.1 GCC<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.4.2 \u5357\u30a2\u30d5\u30ea\u30ab<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.4.3 \u305d\u306e\u4ed6\u306e\u4e2d\u6771 &amp; \u30a2\u30d5\u30ea\u30ab<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          5.6.5 \u5357\u7c73<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.5.1 \u30d6\u30e9\u30b8\u30eb<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.5.2 \u30a2\u30eb\u30bc\u30f3\u30c1\u30f3<\/p>\n<\/li>\n<li class=\"toc-level-4\">\n          5.6.5.3 \u305d\u306e\u4ed6\u306e\u5357\u7c73<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">\n    6. \u7af6\u5408\u60c5\u52e2<\/p>\n<ul>\n<li class=\"toc-level-2\">\n          6.1 \u5e02\u5834\u96c6\u4e2d\u5ea6<\/p>\n<\/li>\n<li class=\"toc-level-2\">\n          6.2 \u5e02\u5834\u30b7\u30a7\u30a2\u5206\u6790<\/p>\n<\/li>\n<li class=\"toc-level-2\">\n          6.3 \u4f01\u696d\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\uff08\u30b0\u30ed\u30fc\u30d0\u30eb\u30ec\u30d9\u30eb\u306e\u6982\u8981\u3001\u5e02\u5834\u30ec\u30d9\u30eb\u306e\u6982\u8981\u3001\u4e3b\u8981\u4e8b\u696d\u30bb\u30b0\u30e1\u30f3\u30c8\u3001\u8ca1\u52d9\u3001\u5f93\u696d\u54e1\u6570\u3001\u4e3b\u8981\u60c5\u5831\u3001\u5e02\u5834\u30e9\u30f3\u30af\u3001\u5e02\u5834\u30b7\u30a7\u30a2\u3001\u88fd\u54c1\u3068\u30b5\u30fc\u30d3\u30b9\u3001\u304a\u3088\u3073\u6700\u8fd1\u306e\u52d5\u5411\u306e\u5206\u6790\u3092\u542b\u3080\uff09<\/p>\n<ul>\n<li class=\"toc-level-3\">\n          6.3.1 \u30b5\u30ce\u30d5\u30a3\uff08\u30b8\u30a7\u30f3\u30b6\u30a4\u30e0\uff09<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.2 \u6b66\u7530\u85ac\u54c1\u5de5\u696d\u682a\u5f0f\u4f1a\u793e<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.3 \u30d0\u30a4\u30aa\u30de\u30ea\u30f3\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30fb\u30a4\u30f3\u30af<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.4 \u30a2\u30df\u30ab\u30b9\u30fb\u30bb\u30e9\u30d4\u30e5\u30fc\u30c6\u30a3\u30af\u30b9<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.5 \u30a6\u30eb\u30c8\u30e9\u30b8\u30a7\u30cb\u30c3\u30af\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30fb\u30a4\u30f3\u30af<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.6 \u30b9\u30d1\u30fc\u30af\u30fb\u30bb\u30e9\u30d4\u30e5\u30fc\u30c6\u30a3\u30af\u30b9<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.7 JCR\u30d5\u30a1\u30fc\u30de\u682a\u5f0f\u4f1a\u793e<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.8 \u30d7\u30ed\u30bf\u30ea\u30c3\u30af\u30b9\u30fb\u30d0\u30a4\u30aa\u30bb\u30e9\u30d4\u30e5\u30fc\u30c6\u30a3\u30af\u30b9<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.9 \u30ad\u30a8\u30fc\u30b7\u30fb\u30d5\u30a1\u30eb\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30c1 S.p.A.<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.10 GC\u30d5\u30a1\u30fc\u30de\uff08\u30b0\u30ea\u30fc\u30f3\u30af\u30ed\u30b9\u793e\uff09<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.11 ISU\u30a2\u30d6\u30b7\u30b9<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.12 \u30c7\u30ca\u30ea\u30fb\u30bb\u30e9\u30d4\u30e5\u30fc\u30c6\u30a3\u30af\u30b9<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.13 \u30ad\u30e3\u30f3\u30d6\u30ea\u30c3\u30b8\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba\u30fb\u30a4\u30f3\u30af<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.14 \u30d5\u30a1\u30fc\u30df\u30f3\u30b0\u30fb\u30b0\u30eb\u30fc\u30d7 N.V.<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.15 SOBI\uff08\u30aa\u30fc\u30d5\u30a1\u30f3\u30fb\u30d0\u30a4\u30aa\u30d3\u30c8\u30e9\u30e0\uff09<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.16 \u30a2\u30d0\u30af\u30bf\u30fb\u30b0\u30eb\u30fc\u30d7 plc<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.17 \u30aa\u30fc\u30c1\u30e3\u30fc\u30c9\u30fb\u30bb\u30e9\u30d4\u30e5\u30fc\u30c6\u30a3\u30af\u30b9<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.18 EUSA\u30d5\u30a1\u30fc\u30de<\/p>\n<\/li>\n<li class=\"toc-level-3\">\n          6.3.19 \u30a4\u30c9\u30eb\u30b7\u30a2\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba<\/p>\n<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">\n    7. \u5e02\u5834\u6a5f\u4f1a\u3068\u5c06\u6765\u5c55\u671b<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u9175\u7d20\u88dc\u5145\u7642\u6cd5\uff08ERT\uff09\u5e02\u5834\u306e\u6982\u8981<\/p>\n<p>\u9175\u7d20\u88dc\u5145\u7642\u6cd5\uff08ERT\uff09\u5e02\u5834\u306f\u30012025\u5e74\u306b\u306f160.1\u5104\u7c73\u30c9\u30eb\u306b\u9054\u3057\u30012030\u5e74\u307e\u3067\u306b247.6\u5104\u7c73\u30c9\u30eb\u3078\u3068\u6210\u9577\u3057\u3001\u5e74\u5e73\u5747\u6210\u9577\u7387\uff08CAGR\uff099.11%\u3092\u8a18\u9332\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u3053\u306e\u6301\u7d9a\u7684\u306a\u62e1\u5927\u306f\u3001\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u306e\u666e\u53ca\u3001\u8a3a\u65ad\u30c4\u30fc\u30eb\u306e\u9ad8\u5ea6\u5316\u3001\u30e9\u30a4\u30bd\u30bd\u30fc\u30e0\u84c4\u7a4d\u75c7\u3078\u306e\u8a8d\u8b58\u5411\u4e0a\u3001\u6280\u8853\u3092\u6d3b\u7528\u3057\u305f\u9175\u7d20\u5de5\u5b66\u306e\u9032\u6b69\u3001\u305d\u3057\u3066\u5728\u5b85\u8f38\u6ce8\u3078\u306e\u79fb\u884c\u304c\u4e3b\u306a\u8981\u56e0\u3068\u306a\u3063\u3066\u3044\u307e\u3059\u3002\u898f\u5236\u5f53\u5c40\u306b\u3088\u308b\u5e0c\u5c11\u75be\u60a3\u6cbb\u7642\u85ac\u306e\u627f\u8a8d\u52a0\u901f\u3084\u3001\u30d0\u30ea\u30e5\u30fc\u30d9\u30fc\u30b9\u5951\u7d04\u306e\u5c0e\u5165\u3082\u5e02\u5834\u3092\u5f62\u6210\u3057\u3066\u3044\u307e\u3059\u3002\u904e\u53bb\u306e\u81b5\u9175\u7d20\u4e0d\u8db3\u304c\u793a\u3057\u305f\u8106\u5f31\u6027\u304b\u3089\u3001\u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u306e\u56de\u5fa9\u529b\u3082\u6226\u7565\u7684\u8ab2\u984c\u3068\u306a\u3063\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u4e3b\u8981\u306a\u5e02\u5834\u52d5\u5411\u3068\u6d1e\u5bdf<\/p>\n<p>\u5e02\u5834\u3092\u727d\u5f15\u3059\u308b\u8981\u56e0\uff1a<\/p>\n<p>1.  \u5e0c\u5c11\u75be\u60a3\u306e\u6709\u75c5\u7387\u5897\u52a0\uff1a \u4e2d\u56fd\u306e\u65b0\u751f\u5150\u30b2\u30ce\u30e0\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u3088\u308a\u3001\u30e9\u30a4\u30bd\u30bd\u30fc\u30e0\u84c4\u7a4d\u75c7\u306e\u6709\u75c5\u7387\u304c\u4e88\u60f3\u4ee5\u4e0a\u306b\u9ad8\u3044\u3053\u3068\u304c\u5224\u660e\u3057\u3001\u672a\u8a3a\u65ad\u60a3\u8005\u5c64\u306e\u5b58\u5728\u304c\u660e\u3089\u304b\u306b\u306a\u308a\u307e\u3057\u305f\u3002\u65e9\u671f\u8a3a\u65ad\u306f\u4e0d\u53ef\u9006\u7684\u306a\u81d3\u5668\u640d\u50b7\u3092\u9632\u304e\u3001\u751f\u6daf\u30b3\u30b9\u30c8\u3092\u524a\u6e1b\u3059\u308b\u305f\u3081\u3001\u4fdd\u967a\u8005\u3082\u4e88\u9632\u7684\u652f\u51fa\u3068\u3057\u3066\u65e9\u671f\u6cbb\u7642\u3092\u91cd\u8996\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n2.  \u653f\u5e9c\u306e\u30a4\u30f3\u30bb\u30f3\u30c6\u30a3\u30d6\u3068\u8cc7\u91d1\u63d0\u4f9b\uff1a \u7c73\u56fdFDA\u306b\u3088\u308b\u5e0c\u5c11\u5c0f\u5150\u75be\u60a3\u6307\u5b9a\uff08M6P Therapeutics\u306e\u4e8b\u4f8b\uff09\u3084\u3001\u6b27\u5dde\u306e\u30aa\u30fc\u30d5\u30a1\u30f3\u30b2\u30ce\u30e0\u7642\u6cd5\u57fa\u91d1\u306e\u63d0\u6848\u306a\u3069\u3001\u653f\u5e9c\u306e\u652f\u63f4\u304c\u958b\u767a\u671f\u9593\u3092\u77ed\u7e2e\u3057\u3001\u5e02\u5834\u7af6\u4e89\u3092\u6fc0\u5316\u3055\u305b\u3066\u3044\u307e\u3059\u3002\u88fd\u9020\u80fd\u529b\u3078\u306e\u76f4\u63a5\u88dc\u52a9\u91d1\u3082\u4f9b\u7d66\u5b89\u5b9a\u6027\u3078\u306e\u4fe1\u983c\u3092\u9ad8\u3081\u3066\u3044\u307e\u3059\u3002<br \/>\n3.  \u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u30d7\u30ed\u30b0\u30e9\u30e0\u306e\u62e1\u5927\uff1a UCSF\u306ePEARL\u8a66\u9a13\u306e\u3088\u3046\u306b\u3001\u51fa\u751f\u524d\u9175\u7d20\u7642\u6cd5\u304c\u5c0e\u5165\u3055\u308c\u3001\u5305\u62ec\u7684\u306a\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u30d1\u30cd\u30eb\u306e\u8ffd\u52a0\u306b\u3088\u308a\u3001\u75be\u60a3\u306e\u65e9\u671f\u767a\u898b\u304c\u53ef\u80fd\u3068\u306a\u308a\u3001\u795e\u7d4c\u5b66\u7684\u30fb\u9aa8\u683c\u7684\u640d\u50b7\u306e\u56de\u907f\u306b\u8ca2\u732e\u3057\u3066\u3044\u307e\u3059\u3002\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u8cbb\u7528\u306f\u5408\u4f75\u75c7\u56de\u907f\u306b\u3088\u308a3\u5e74\u4ee5\u5185\u306b\u76f8\u6bba\u3055\u308c\u308b\u3068\u3044\u3046\u7d4c\u6e08\u30e2\u30c7\u30eb\u3082\u3001\u30ea\u30bd\u30fc\u30b9\u304c\u9650\u3089\u308c\u305f\u5730\u57df\u3067\u652f\u6301\u3055\u308c\u3066\u3044\u307e\u3059\u3002<br \/>\n4.  \u60a3\u8005\u4e2d\u5fc3\u306e\u30c7\u30ea\u30d0\u30ea\u30fc\u3078\u306e\u79fb\u884c\uff1a \u30a4\u30bf\u30ea\u30a2\u306e\u30b3\u30db\u30fc\u30c8\u7814\u7a76\u3067\u306f\u3001\u9175\u7d20\u8f38\u6ce8\u3092\u75c5\u9662\u304b\u3089\u5728\u5b85\u3078\u79fb\u884c\u3059\u308b\u3053\u3068\u3067\u3001\u76f4\u63a5\u30b3\u30b9\u30c8\u304c25\uff5e50%\u524a\u6e1b\u3055\u308c\u3001\u30a2\u30c9\u30d2\u30a2\u30e9\u30f3\u30b9\u3068\u60a3\u8005\u30b9\u30c8\u30ec\u30b9\u306e\u8efd\u6e1b\u304c\u5831\u544a\u3055\u308c\u3066\u3044\u307e\u3059\u3002COVID-19\u30d1\u30f3\u30c7\u30df\u30c3\u30af\u4e2d\u306e\u9060\u9694\u30e2\u30cb\u30bf\u30ea\u30f3\u30b0\u6280\u8853\u306e\u6d3b\u7528\u3082\u3001\u5728\u5b85\u6295\u4e0e\u306e\u5b89\u5168\u6027\u3092\u78ba\u7acb\u3057\u3001\u60a3\u8005\u4e2d\u5fc3\u30e2\u30c7\u30eb\u3092\u5b9a\u7740\u3055\u305b\u307e\u3057\u305f\u3002<br \/>\n5.  \u9175\u7d20\u5de5\u5b66\u306b\u304a\u3051\u308b\u6280\u8853\u9032\u6b69\uff1a \u9175\u7d20\u306e\u534a\u6e1b\u671f\u5ef6\u9577\u3001\u514d\u75ab\u539f\u6027\u4f4e\u6e1b\u3001\u8f38\u6ce8\u983b\u5ea6\u524a\u6e1b\u3092\u76ee\u6307\u3057\u305fPEG\u5316\u3084\u7cd6\u9396\u6539\u5909\u306a\u3069\u306e\u6280\u8853\u9769\u65b0\u304c\u5e02\u5834\u6210\u9577\u306b\u5bc4\u4e0e\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n6.  \u9769\u65b0\u7684\u306a\u511f\u9084\u30e2\u30c7\u30eb\uff1a \u6210\u679c\u30d9\u30fc\u30b9\u306e\u5951\u7d04\u306a\u3069\u3001\u65b0\u3057\u3044\u511f\u9084\u30e2\u30c7\u30eb\u304c\u5c0e\u5165\u3055\u308c\u3001\u6cbb\u7642\u3078\u306e\u30a2\u30af\u30bb\u30b9\u3092\u6539\u5584\u3057\u3001\u5e02\u5834\u306e\u6210\u9577\u3092\u4fc3\u9032\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u5e02\u5834\u306e\u6291\u5236\u8981\u56e0\uff1a<\/p>\n<p>1.  \u9ad8\u984d\u306a\u6cbb\u7642\u8cbb\uff1a \u7c73\u56fd\u3067\u306f\u60a3\u8005\u4e00\u4eba\u3042\u305f\u308a\u5e74\u959320\u4e07\uff5e30\u4e07\u7c73\u30c9\u30eb\u306e\u8cbb\u7528\u304c\u304b\u304b\u308a\u3001\u65b0\u8208\u56fd\u3067\u306e\u666e\u53ca\u3092\u59a8\u3052\u3066\u3044\u307e\u3059\u3002\u6b27\u5dde\u3067\u3082\u511f\u9084\u7387\u306b\u5927\u304d\u306a\u5dee\u304c\u3042\u308a\u3001\u9700\u8981\u306e\u5206\u65ad\u3068\u53ce\u76ca\u306e\u4e88\u6e2c\u53ef\u80fd\u6027\u3092\u4f4e\u4e0b\u3055\u305b\u3066\u3044\u307e\u3059\u3002<br \/>\n2.  \u514d\u75ab\u539f\u6027\u306e\u61f8\u5ff5\uff1a \u9175\u7d20\u6cbb\u7642\u60a3\u8005\u306e\u534a\u6570\u304c\u6297\u85ac\u7269\u6297\u4f53\u3092\u7523\u751f\u3057\u3001\u6cbb\u7642\u52b9\u679c\u306e\u6e1b\u5f31\u3084\u8f38\u6ce8\u53cd\u5fdc\u3092\u5f15\u304d\u8d77\u3053\u3059\u3053\u3068\u304c\u3042\u308a\u307e\u3059\u3002\u30d0\u30a4\u30aa\u30b7\u30df\u30e9\u30fc\u958b\u767a\u306b\u304a\u3044\u3066\u3082\u3001\u88fd\u9020\u4e0a\u306e\u308f\u305a\u304b\u306a\u5dee\u7570\u304c\u514d\u75ab\u539f\u6027\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u3092\u5909\u5316\u3055\u305b\u308b\u53ef\u80fd\u6027\u304c\u3042\u308a\u3001\u898f\u5236\u5f53\u5c40\u306e\u76e3\u8996\u304c\u53b3\u3057\u304f\u306a\u3063\u3066\u3044\u307e\u3059\u3002<br \/>\n3.  \u65b0\u8208\u6cbb\u7642\u6cd5\u3068\u306e\u7af6\u5408\uff1a \u907a\u4f1d\u5b50\u6cbb\u7642\u306a\u3069\u3001\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u306b\u4ee3\u308f\u308b\u53ef\u80fd\u6027\u306e\u3042\u308b\u65b0\u3057\u3044\u6cbb\u7642\u6cd5\u306e\u767b\u5834\u304c\u3001\u9577\u671f\u7684\u306b\u5e02\u5834\u306e\u6210\u9577\u3092\u6291\u5236\u3059\u308b\u53ef\u80fd\u6027\u304c\u3042\u308a\u307e\u3059\u3002<br \/>\n4.  \u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u306e\u8ab2\u984c\uff1a \u4e16\u754c\u7684\u306a\u81b5\u9175\u7d20\u4e0d\u8db3\u306e\u4e8b\u4f8b\u304c\u793a\u3059\u3088\u3046\u306b\u3001\u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u306e\u8106\u5f31\u6027\u306f\u6cbb\u7642\u306e\u7d99\u7d9a\u6027\u3092\u8105\u304b\u3057\u3001\u5e02\u5834\u306b\u60aa\u5f71\u97ff\u3092\u4e0e\u3048\u308b\u53ef\u80fd\u6027\u304c\u3042\u308a\u307e\u3059\u3002<\/p>\n<p>\u30bb\u30b0\u30e1\u30f3\u30c8\u5206\u6790<\/p>\n<p>*   \u9175\u7d20\u30bf\u30a4\u30d7\u5225\uff1a \u30a4\u30df\u30b0\u30eb\u30bb\u30e9\u30fc\u30bc\u304c2024\u5e74\u306b38.65%\u306e\u5e02\u5834\u30b7\u30a7\u30a2\u3092\u5360\u3081\u3001\u30b4\u30fc\u30b7\u30a7\u75c5\u6cbb\u7642\u306b\u304a\u3051\u308b\u78ba\u56fa\u305f\u308b\u5730\u4f4d\u3092\u7dad\u6301\u3057\u3066\u3044\u307e\u3059\u3002\u3057\u304b\u3057\u3001\u30a2\u30d0\u30eb\u30b0\u30eb\u30b3\u30b7\u30c0\u30fc\u30bc\u30a2\u30eb\u30d5\u30a1\u306f\u30dd\u30f3\u30da\u75c5\u6cbb\u7642\u306b\u304a\u3051\u308b\u30ea\u30bd\u30bd\u30fc\u30e0\u6a19\u7684\u5316\u306e\u5f37\u5316\u306b\u3088\u308a\u30012030\u5e74\u307e\u3067\u306b11.56%\u306eCAGR\u3067\u6210\u9577\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002PEG\u5316\u3084\u7cd6\u9396\u6539\u5909\u3055\u308c\u305f\u6b21\u4e16\u4ee3\u9175\u7d20\u88fd\u5264\u304c\u3001\u534a\u6e1b\u671f\u306e\u5ef6\u9577\u3001\u514d\u75ab\u539f\u6027\u306e\u4f4e\u6e1b\u3001\u8f38\u6ce8\u983b\u5ea6\u306e\u524a\u6e1b\u3092\u7d04\u675f\u3057\u3001\u6025\u901f\u306a\u62e1\u5927\u304c\u898b\u8fbc\u307e\u308c\u307e\u3059\u3002<br \/>\n*   \u7528\u9014\u5225\uff1a \u30b4\u30fc\u30b7\u30a7\u75c5\u6cbb\u7642\u304c2024\u5e74\u306b43.67%\u306e\u5e02\u5834\u898f\u6a21\u3092\u5360\u3081\u3001\u8907\u6570\u306e\u627f\u8a8d\u6e08\u307f\u85ac\u5264\u3068\u78ba\u7acb\u3055\u308c\u305f\u6295\u4e0e\u30a2\u30eb\u30b4\u30ea\u30ba\u30e0\u306b\u652f\u3048\u3089\u308c\u3066\u3044\u307e\u3059\u3002\u30dd\u30f3\u30da\u75c5\u306f\u3001\u30b7\u30d1\u30b0\u30eb\u30b3\u30b7\u30c0\u30fc\u30bc\u30a2\u30eb\u30d5\u30a1\u3068\u30df\u30b0\u30eb\u30b9\u30bf\u30c3\u30c8\u306e\u4f75\u7528\u7642\u6cd5\u304c\u5358\u5264\u7642\u6cd5\u3092\u4e0a\u56de\u308b\u6210\u7e3e\u3092\u793a\u3057\u30012030\u5e74\u307e\u3067\u306b11.43%\u306eCAGR\u3067\u6210\u9577\u3059\u308b\u3068\u4e88\u60f3\u3055\u308c\u3066\u3044\u307e\u3059\u3002FLT201\u306a\u3069\u306e\u65b0\u8208\u907a\u4f1d\u5b50\u6cbb\u7642\u306f\u3001\u9577\u671f\u7684\u306b\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u306e\u9700\u8981\u3092\u5727\u8feb\u3059\u308b\u53ef\u80fd\u6027\u304c\u3042\u308a\u307e\u3059\u3002<br \/>\n*   \u6295\u4e0e\u7d4c\u8def\u5225\uff1a \u9759\u8108\u5185\u8f38\u6ce8\u304c2024\u5e74\u306b92.34%\u306e\u53ce\u76ca\u30b7\u30a7\u30a2\u3092\u5360\u3081\u3066\u3044\u307e\u3059\u304c\u3001\u60a3\u8005\u306e\u81ea\u5f8b\u6027\u3068\u8a3a\u5bdf\u6642\u9593\u306e\u77ed\u7e2e\u3092\u597d\u3080\u50be\u5411\u304b\u3089\u3001\u76ae\u4e0b\u6295\u4e0e\u88fd\u5264\u304c10.45%\u306eCAGR\u3067\u6210\u9577\u3057\u3066\u3044\u307e\u3059\u3002\u958b\u767a\u8005\u306f\u3001IV\u88fd\u5264\u3068\u306e\u751f\u7269\u5b66\u7684\u540c\u7b49\u6027\u3092\u78ba\u4fdd\u3059\u308b\u305f\u3081\u3001\u7c98\u5ea6\u3001\u6d78\u900f\u5727\u3001\u5b89\u5b9a\u5264\u542b\u6709\u91cf\u3092\u6700\u9069\u5316\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u88fd\u5264\u5225\uff1a \u6a19\u6e96\u7d44\u63db\u3048\u9175\u7d20\u304c2024\u5e74\u306b55.34%\u306e\u30b7\u30a7\u30a2\u3092\u5360\u3081\u3066\u3044\u307e\u3059\u304c\u3001PEG\u5316\u88fd\u5264\u306f\u534a\u6e1b\u671f\u3092\u5ef6\u9577\u3057\u3001\u6295\u4e0e\u983b\u5ea6\u3092\u6e1b\u3089\u3059\u3053\u3068\u306710.23%\u306eCAGR\u3067\u6210\u9577\u3057\u3066\u3044\u307e\u3059\u3002\u9175\u7d20\u3092\u6297\u4f53\u65ad\u7247\u306b\u878d\u5408\u3055\u305b\u308b\u878d\u5408\u30bf\u30f3\u30d1\u30af\u8cea\u6280\u8853\u3082\u7d44\u7e54\u6d78\u900f\u6027\u3092\u6539\u5584\u3057\u3001\u6210\u9577\u306b\u8ca2\u732e\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u30a8\u30f3\u30c9\u30e6\u30fc\u30b6\u30fc\u5225\uff1a \u75c5\u9662\u304a\u3088\u3073\u5c02\u9580\u30af\u30ea\u30cb\u30c3\u30af\u304c2024\u5e74\u306b72.56%\u306e\u53ce\u76ca\u3092\u5360\u3081\u3066\u3044\u307e\u3059\u304c\u3001\u5728\u5b85\u533b\u7642\u306f25\uff5e50%\u306e\u30b3\u30b9\u30c8\u512a\u4f4d\u6027\u3068\u512a\u308c\u305f\u60a3\u8005\u5831\u544a\u30a2\u30a6\u30c8\u30ab\u30e0\u306b\u3088\u308a\u300112.56%\u306eCAGR\u3067\u6700\u3082\u6025\u901f\u306b\u6210\u9577\u3057\u3066\u3044\u307e\u3059\u3002\u30c7\u30b8\u30bf\u30eb\u30a2\u30c9\u30d2\u30a2\u30e9\u30f3\u30b9\u30c4\u30fc\u30eb\u304c\u5728\u5b85\u8f38\u6ce8\u306e\u511f\u9084\u3092\u5f8c\u62bc\u3057\u3057\u3001\u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u306e\u518d\u69cb\u7bc9\u3092\u4fc3\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u5730\u7406\u7684\u5206\u6790<\/p>\n<p>*   \u5317\u7c73\uff1a 2024\u5e74\u306b38.54%\u306e\u30b7\u30a7\u30a2\u3092\u7dad\u6301\u3057\u3001\u6f64\u6ca2\u306a\u4fdd\u967a\u5236\u5ea6\u3068\u5e0c\u5c11\u75be\u60a3\u627f\u8a8d\u3092\u52a0\u901f\u3059\u308bFDA\uff08\u30ec\u30e1\u30eb\u30c7\u30a3\u306e\u4e8b\u4f8b\uff09\u306e\u6069\u6075\u3092\u53d7\u3051\u3066\u3044\u307e\u3059\u3002\u6210\u679c\u30d9\u30fc\u30b9\u306e\u5951\u7d04\u304c\u666e\u53ca\u3057\u3001\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u306e\u7fa9\u52d9\u5316\u3082\u65e9\u671f\u8a3a\u65ad\u3068\u6cbb\u7642\u958b\u59cb\u3092\u4fc3\u9032\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u6b27\u5dde\uff1a \u30a2\u30af\u30bb\u30b9\u72b6\u6cc1\u306f\u591a\u69d8\u3067\u3001\u30c7\u30f3\u30de\u30fc\u30af\u304c88%\u306e\u8cbb\u7528\u3092\u511f\u9084\u3059\u308b\u4e00\u65b9\u3067\u3001\u30dd\u30fc\u30e9\u30f3\u30c9\u306f27%\u306b\u3068\u3069\u307e\u308a\u3001\u53ce\u76ca\u306b\u3070\u3089\u3064\u304d\u304c\u751f\u3058\u3066\u3044\u307e\u3059\u3002\u6b27\u5dde\u533b\u85ac\u54c1\u5e81\uff08EMA\uff09\u306b\u3088\u308b\u96c6\u4e2d\u627f\u8a8d\u306f\u7533\u8acb\u3092\u7c21\u7d20\u5316\u3057\u307e\u3059\u304c\u3001\u627f\u8a8d\u5f8c\u306e\u4fa1\u683c\u4ea4\u6e09\u306b\u306f\u6570\u5e74\u3092\u8981\u3059\u308b\u3053\u3068\u3082\u3042\u308a\u307e\u3059\u3002<br \/>\n*   \u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\uff1a 10.45%\u306eCAGR\u3067\u6700\u3082\u6025\u901f\u306b\u6210\u9577\u3057\u3066\u3044\u308b\u5730\u57df\u3067\u3059\u3002\u7a4d\u6975\u7684\u306a\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u3001\u6240\u5f97\u6c34\u6e96\u306e\u4e0a\u6607\u3001\u5730\u57df\u751f\u7523\u62e0\u70b9\u306e\u78ba\u7acb\u304c\u6210\u9577\u3092\u5f8c\u62bc\u3057\u3057\u3066\u3044\u307e\u3059\u3002\u4e2d\u56fd\u306e\u30b2\u30ce\u30e0\u30d1\u30cd\u30eb\u306f\u4e88\u60f3\u4ee5\u4e0a\u306e\u30e9\u30a4\u30bd\u30bd\u30fc\u30e0\u75be\u60a3\u767a\u751f\u7387\u3092\u660e\u3089\u304b\u306b\u3057\u3001\u5730\u65b9\u81ea\u6cbb\u4f53\u306b\u3088\u308b\u6cbb\u7642\u8cbb\u88dc\u52a9\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u3064\u306a\u304c\u3063\u3066\u3044\u307e\u3059\u3002\u65e5\u672c\u3067\u306e\u30d1\u30d3\u30ca\u30d5\u30b9\u30d7\u30a2\u30eb\u30d5\u30a1\uff08MPS II\uff09\u3084\u30a2\u30bb\u30ce\u30a4\u30e9\u30df\u30f3\u9178\uff08GNE\u30df\u30aa\u30d1\u30c1\u30fc\uff09\u306e\u627f\u8a8d\u306f\u3001\u6700\u5148\u7aef\u306e\u6cbb\u7642\u6cd5\u306b\u5bfe\u3059\u308b\u898f\u5236\u5f53\u5c40\u306e\u958b\u653e\u6027\u3092\u793a\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u7af6\u5408\u72b6\u6cc1<\/p>\n<p>\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u5e02\u5834\u306f\u4e2d\u7a0b\u5ea6\u306e\u7d71\u5408\u5ea6\u3092\u4fdd\u3063\u3066\u304a\u308a\u3001Sanofi\uff08Genzyme\uff09\u3001Takeda\u3001BioMarin\u304c\u5f37\u56fa\u306a\u81e8\u5e8a\u7d4c\u9a13\u3001\u7279\u8a31\u3001\u30b0\u30ed\u30fc\u30d0\u30eb\u306a\u6d41\u901a\u7db2\u3092\u80cc\u666f\u306b\u4e3b\u5c0e\u3057\u3066\u3044\u307e\u3059\u3002BioMarin\u306f2025\u5e74\u7b2c1\u56db\u534a\u671f\u306b\u9175\u7d20\u8cc7\u7523\u304b\u30894\u51048400\u4e07\u7c73\u30c9\u30eb\u306e\u53ce\u76ca\u3092\u4e0a\u3052\u300115%\u306e\u6210\u9577\u3092\u8a18\u9332\u3057\u307e\u3057\u305f\u3002\u65e2\u5b58\u4f01\u696d\u306fPEG\u5316\u3001\u878d\u5408\u30bf\u30f3\u30d1\u30af\u8cea\u8a2d\u8a08\u3001\u8cb7\u53ce\u3092\u901a\u3058\u3066\u30dd\u30fc\u30c8\u30d5\u30a9\u30ea\u30aa\u3092\u5237\u65b0\u3057\u3001\u5c02\u9580\u85ac\u5c40\u3084\u5728\u5b85\u533b\u7642\u63d0\u4f9b\u8005\u3068\u306e\u6226\u7565\u7684\u63d0\u643a\u3092\u5f37\u5316\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>Spur Therapeutics\u306eFLT201\u3084REGENXBIO\u306eRGX-121\u306e\u3088\u3046\u306a\u907a\u4f1d\u5b50\u6cbb\u7642\u306f\u3001\u6301\u7d9a\u7684\u306a\u9175\u7d20\u767a\u73fe\u3092\u53ef\u80fd\u306b\u3057\u3001\u6162\u6027\u8f38\u6ce8\u9700\u8981\u3092\u4fb5\u98df\u3059\u308b\u53ef\u80fd\u6027\u3092\u79d8\u3081\u3066\u3044\u307e\u3059\u3002REGENXBIO\u3068\u65e5\u672c\u65b0\u85ac\u306e\u63d0\u643a\uff081\u51041000\u4e07\u7c73\u30c9\u30eb\u306e\u524d\u6255\u3044\u91d1\u3068\u6700\u59277\u5104\u7c73\u30c9\u30eb\u306e\u30de\u30a4\u30eb\u30b9\u30c8\u30fc\u30f3\uff09\u306f\u3001\u30d0\u30a4\u30aa\u30c6\u30af\u30ce\u30ed\u30b8\u30fc\u9769\u65b0\u4f01\u696d\u304c\u77e5\u7684\u8ca1\u7523\u3068\u5730\u57df\u5546\u696d\u5316\u529b\u3092\u7d44\u307f\u5408\u308f\u305b\u3001\u5e02\u5834\u53c2\u5165\u3092\u52a0\u901f\u3059\u308b\u4f8b\u3067\u3059\u3002\u30d0\u30a4\u30aa\u30b7\u30df\u30e9\u30fc\u958b\u767a\u4f01\u696d\u306f\u7279\u8a31\u5207\u308c\u3092\u72d9\u3063\u3066\u3044\u307e\u3059\u304c\u3001\u9ad8\u3044\u5206\u6790\u7684\u30fb\u514d\u75ab\u539f\u6027\u306b\u95a2\u3059\u308b\u30cf\u30fc\u30c9\u30eb\u306b\u76f4\u9762\u3057\u3066\u304a\u308a\u3001\u5f53\u9762\u306f\u65e2\u5b58\u4f01\u696d\u304c\u512a\u4f4d\u3092\u4fdd\u3064\u3067\u3057\u3087\u3046\u3002<\/p>\n<p>\u88fd\u9020\u898f\u6a21\u3082\u91cd\u8981\u306a\u7af6\u4e89\u8981\u56e0\u3067\u3042\u308a\u3001Samsung Biologics\u306f2025\u5e74\u307e\u3067\u306b784,000L\u306e\u751f\u7523\u80fd\u529b\u3092\u8a08\u753b\u3057\u3001\u8fc5\u901f\u306a\u30bf\u30fc\u30f3\u30a2\u30e9\u30a6\u30f3\u30c9\u3068\u4f4e\u30b3\u30b9\u30c8\u5316\u3092\u76ee\u6307\u3057\u3066\u3044\u307e\u3059\u3002\u4f9b\u7d66\u80fd\u529b\u306e\u78ba\u4fdd\u306f\u3001\u904e\u53bb\u306e\u81b5\u9175\u7d20\u4e0d\u8db3\u306e\u3088\u3046\u306a\u4e8b\u614b\u304b\u3089\u9867\u5ba2\u3092\u4fdd\u8b77\u3057\u3001\u5b89\u5b9a\u4f9b\u7d66\u3092\u4fdd\u8a3c\u3067\u304d\u308b\u4f01\u696d\u306f\u3001\u4fdd\u967a\u8005\u3084\u533b\u7642\u30b7\u30b9\u30c6\u30e0\u3068\u306e\u8907\u6570\u5e74\u5951\u7d04\u3092\u7372\u5f97\u3057\u3001\u5e02\u5834\u30b7\u30a7\u30a2\u3092\u5f37\u5316\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u696d\u754c\u306e\u4e3b\u8981\u4f01\u696d<\/p>\n<p>*   Sanofi (Genzyme)<br \/>\n*   Takeda Pharmaceutical Co. Ltd<br \/>\n*   BioMarin Pharmaceutical Inc.<br \/>\n*   Amicus Therapeutics<br \/>\n*   Ultragenyx Pharmaceutical Inc.<\/p>\n<p>\u6700\u8fd1\u306e\u696d\u754c\u52d5\u5411<\/p>\n<p>*   2025\u5e743\u6708\uff1a Ultragenyx\u306f2025\u5e74\u7b2c1\u56db\u534a\u671f\u306b1\u51043900\u4e07\u7c73\u30c9\u30eb\u306e\u53ce\u76ca\u3092\u5831\u544a\u3057\u3001\u30b5\u30f3\u30d5\u30a3\u30ea\u30c3\u30dd\u75c7\u5019\u7fa4\u5411\u3051\u907a\u4f1d\u5b50\u6cbb\u7642UX111\u306ePDUFA\u30a2\u30af\u30b7\u30e7\u30f3\u65e5\u4ed8\u304c2025\u5e748\u670818\u65e5\u306b\u8a2d\u5b9a\u3055\u308c\u307e\u3057\u305f\u3002<br \/>\n*   2025\u5e743\u6708\uff1a Sanofi\u306f\u3001\u8840\u53cb\u75c5A\u304a\u3088\u3073B\u306b\u5bfe\u3059\u308b\u521d\u306e\u6297\u30c8\u30ed\u30f3\u30d3\u30f3\u4f4e\u4e0b\u7642\u6cd5\u3067\u3042\u308bQfitlia\uff08\u30d5\u30a3\u30c4\u30b7\u30e9\u30f3\uff09\u306eFDA\u627f\u8a8d\u3092\u7372\u5f97\u3057\u307e\u3057\u305f\u3002\u5e74\u9593\u308f\u305a\u304b6\u56de\u306e\u6ce8\u5c04\u3067\u6295\u4e0e\u53ef\u80fd\u3067\u3059\u3002<br \/>\n*   2025\u5e742\u6708\uff1a FDA\u306f\u3001\u8133\u8171\u9ec4\u8272\u816b\u75c7\u306e\u521d\u306e\u6cbb\u7642\u85ac\u3068\u3057\u3066Ctexli\uff08\u30b1\u30ce\u30b8\u30aa\u30fc\u30eb\uff09\u3092\u627f\u8a8d\u3057\u307e\u3057\u305f\u3002\u3053\u308c\u306b\u3088\u308a\u3001\u8840\u6f3f\u30b3\u30ec\u30b9\u30bf\u30ce\u30fc\u30eb\u3068\u5c3f\u4e2d\u30d0\u30a4\u30aa\u30de\u30fc\u30ab\u30fc\u304c\u6e1b\u5c11\u3057\u307e\u3059\u3002<br \/>\n*   2025\u5e742\u6708\uff1a REGENXBIO\u3068\u65e5\u672c\u65b0\u85ac\u306f\u3001RGX-121\u304a\u3088\u3073RGX-111 MPS\u6cbb\u7642\u85ac\u306b\u95a2\u3059\u308b\u72ec\u5360\u7684\u63d0\u643a\u3092\u7de0\u7d50\u3057\u307e\u3057\u305f\u3002\u524d\u6255\u3044\u91d11\u51041000\u4e07\u7c73\u30c9\u30eb\u3068\u3001\u6700\u59277\u5104\u7c73\u30c9\u30eb\u306e\u30de\u30a4\u30eb\u30b9\u30c8\u30fc\u30f3\u304c\u542b\u307e\u308c\u307e\u3059\u3002<br \/>\n*   2025\u5e741\u6708\uff1a FDA\u306fPOMBILITI\u306e\u7279\u8a31\u5ef6\u9577\u306b\u95a2\u3059\u308b\u898f\u5236\u5be9\u67fb\u671f\u9593\u3092\u6c7a\u5b9a\u3057\u30012025\u5e7412\u6708\u307e\u3067\u610f\u898b\u3092\u52df\u96c6\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u9175\u7d20\u88dc\u5145\u7642\u6cd5\uff08Enzyme Replacement Therapy, ERT\uff09\u5e02\u5834\u306b\u95a2\u3059\u308b\u672c\u30ec\u30dd\u30fc\u30c8\u306f\u3001\u305d\u306e\u5e02\u5834\u306e\u5b9a\u7fa9\u3001\u7bc4\u56f2\u3001\u8abf\u67fb\u65b9\u6cd5\u3001\u5e02\u5834\u306e\u52d5\u5411\u3001\u4e88\u6e2c\u3001\u7af6\u4e89\u74b0\u5883\u3001\u304a\u3088\u3073\u5c06\u6765\u306e\u6a5f\u4f1a\u306b\u3064\u3044\u3066\u5305\u62ec\u7684\u306b\u5206\u6790\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>1. \u5e02\u5834\u306e\u5b9a\u7fa9\u3068\u7bc4\u56f2<br \/>\n\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u5e02\u5834\u306f\u3001\u30e9\u30a4\u30bd\u30be\u30fc\u30e0\u84c4\u7a4d\u75c7\u3084\u4ee3\u8b1d\u6027\u75be\u60a3\u306b\u304a\u3051\u308b\u7279\u5b9a\u306e\u751f\u4f53\u5185\u6b20\u4e4f\u3092\u88dc\u3046\u305f\u3081\u306b\u6295\u4e0e\u3055\u308c\u308b\u3001\u51e6\u65b9\u7b8b\u30d9\u30fc\u30b9\u306e\u751f\u7269\u6d3b\u6027\u9175\u7d20\u304b\u3089\u751f\u3058\u308b\u4e16\u754c\u7684\u306a\u53ce\u76ca\u3068\u3057\u3066\u5b9a\u7fa9\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u3053\u306e\u8abf\u67fb\u306e\u7bc4\u56f2\u306b\u306f\u3001\u5e02\u8ca9\u306e\u6d88\u5316\u9175\u7d20\u30d6\u30ec\u30f3\u30c9\u3001\u8abf\u5408\u88fd\u5264\u3001\u304a\u3088\u3073\u524d\u81e8\u5e8a\u6bb5\u968e\u306b\u3042\u308b\u907a\u4f1d\u5b50\u7de8\u96c6\u9175\u7d20\u306f\u542b\u307e\u308c\u3066\u3044\u307e\u305b\u3093\u3002<\/p>\n<p>2. \u30a8\u30b0\u30bc\u30af\u30c6\u30a3\u30d6\u30b5\u30de\u30ea\u30fc\u3068\u5e02\u5834\u898f\u6a21\u30fb\u6210\u9577\u4e88\u6e2c<br \/>\n\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u5e02\u5834\u306f\u30012025\u5e74\u306b\u306f160.1\u5104\u7c73\u30c9\u30eb\u3068\u8a55\u4fa1\u3055\u308c\u3066\u304a\u308a\u30012030\u5e74\u307e\u3067\u306b247.6\u5104\u7c73\u30c9\u30eb\u306b\u9054\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u3053\u306e\u6210\u9577\u306f\u3001\u5e0c\u5c11\u75be\u60a3\u306e\u6709\u75c5\u7387\u5897\u52a0\u3001\u653f\u5e9c\u306e\u30a4\u30f3\u30bb\u30f3\u30c6\u30a3\u30d6\u3001\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u30d7\u30ed\u30b0\u30e9\u30e0\u306e\u62e1\u5927\u3001\u60a3\u8005\u4e2d\u5fc3\u306e\u30c7\u30ea\u30d0\u30ea\u30fc\u3078\u306e\u79fb\u884c\u3001\u9175\u7d20\u5de5\u5b66\u306b\u304a\u3051\u308b\u6280\u8853\u9032\u6b69\u3001\u304a\u3088\u3073\u9769\u65b0\u7684\u306a\u511f\u9084\u30e2\u30c7\u30eb\u3068\u3044\u3063\u305f\u8907\u6570\u306e\u8981\u56e0\u306b\u3088\u3063\u3066\u63a8\u9032\u3055\u308c\u3066\u3044\u307e\u3059\u3002<br \/>\n\u6cbb\u7642\u9818\u57df\u5225\u3067\u306f\u3001\u30b4\u30fc\u30b7\u30a7\u75c5\u306e\u7528\u9014\u304c43.67%\u306e\u5e02\u5834\u30b7\u30a7\u30a2\u3092\u5360\u3081\u3001\u8907\u6570\u306e\u627f\u8a8d\u6e08\u307f\u9175\u7d20\u3068\u6210\u719f\u3057\u305f\u6cbb\u7642\u30d7\u30ed\u30c8\u30b3\u30eb\u306b\u3088\u308a\u5e02\u5834\u3092\u30ea\u30fc\u30c9\u3057\u3066\u3044\u307e\u3059\u3002\u5730\u57df\u5225\u3067\u306f\u3001\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\u5730\u57df\u304c\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u306e\u62e1\u5927\u3001\u4fdd\u967a\u9069\u7528\u7bc4\u56f2\u306e\u62e1\u5927\u3001\u304a\u3088\u3073\u73fe\u5730\u88fd\u9020\u80fd\u529b\u306e\u5411\u4e0a\u306b\u3088\u308a\u300110.45%\u3068\u3044\u3046\u6700\u3082\u9ad8\u3044\u5e74\u5e73\u5747\u6210\u9577\u7387\uff08CAGR\uff09\u3092\u793a\u3059\u3068\u898b\u8fbc\u307e\u308c\u3066\u3044\u307e\u3059\u3002<br \/>\n\u9ad8\u984d\u306a\u6cbb\u7642\u8cbb\u3078\u306e\u5bfe\u5fdc\u3068\u3057\u3066\u3001\u652f\u6255\u8005\u306f\u6e2c\u5b9a\u53ef\u80fd\u306a\u81e8\u5e8a\u6539\u5584\u306b\u511f\u9084\u3092\u7d50\u3073\u3064\u3051\u308b\u30d0\u30ea\u30e5\u30fc\u30d9\u30fc\u30b9\u5951\u7d04\u3084\u6210\u679c\u30d9\u30fc\u30b9\u5951\u7d04\u3092\u63a1\u7528\u3059\u308b\u50be\u5411\u306b\u3042\u308a\u307e\u3059\u3002\u307e\u305f\u3001\u60a3\u8005\u30b1\u30a2\u30e2\u30c7\u30eb\u306e\u5909\u5316\u3068\u3057\u3066\u3001\u5728\u5b85\u6ce8\u5165\u304c\u6ce8\u76ee\u3092\u96c6\u3081\u3066\u304a\u308a\u3001\u76f4\u63a5\u6cbb\u7642\u8cbb\u309225\uff5e50%\u524a\u6e1b\u3057\u3001\u75c5\u9662\u74b0\u5883\u3068\u6bd4\u8f03\u3057\u3066\u30a2\u30c9\u30d2\u30a2\u30e9\u30f3\u30b9\u3092\u5411\u4e0a\u3055\u305b\u308b\u52b9\u679c\u304c\u671f\u5f85\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u5c06\u6765\u306e\u7834\u58ca\u7684\u30a4\u30ce\u30d9\u30fc\u30b7\u30e7\u30f3\u3068\u3057\u3066\u306f\u3001FLT201\u3084RGX-121\u306a\u3069\u306e\u907a\u4f1d\u5b50\u6cbb\u7642\u304c\u3001\u6301\u7d9a\u7684\u306a\u5358\u56de\u6295\u4e0e\u306b\u3088\u308b\u6cbb\u7642\u3092\u63d0\u4f9b\u3057\u3001\u751f\u6daf\u306b\u308f\u305f\u308b\u6ce8\u5165\u306e\u9700\u8981\u3092\u6e1b\u5c11\u3055\u305b\u308b\u53ef\u80fd\u6027\u3092\u79d8\u3081\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>3. \u5e02\u5834\u306e\u63a8\u9032\u8981\u56e0<br \/>\n\u5e02\u5834\u306e\u6210\u9577\u3092\u727d\u5f15\u3059\u308b\u4e3b\u306a\u8981\u56e0\u306f\u4ee5\u4e0b\u306e\u901a\u308a\u3067\u3059\u3002<br \/>\n*   \u5e0c\u5c11\u75be\u60a3\u306e\u6709\u75c5\u7387\u5897\u52a0: \u8a3a\u65ad\u6280\u8853\u306e\u9032\u6b69\u3068\u610f\u8b58\u306e\u5411\u4e0a\u306b\u3088\u308a\u3001\u5e0c\u5c11\u75be\u60a3\u306e\u60a3\u8005\u6570\u304c\u5897\u52a0\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u653f\u5e9c\u306e\u30a4\u30f3\u30bb\u30f3\u30c6\u30a3\u30d6\u3068\u8cc7\u91d1\u63d0\u4f9b: \u5e0c\u5c11\u75be\u60a3\u6cbb\u7642\u85ac\u306e\u958b\u767a\u3092\u4fc3\u9032\u3059\u308b\u305f\u3081\u306e\u653f\u5e9c\u306b\u3088\u308b\u512a\u9047\u63aa\u7f6e\u3084\u7814\u7a76\u8cc7\u91d1\u304c\u5e02\u5834\u3092\u5f8c\u62bc\u3057\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u30d7\u30ed\u30b0\u30e9\u30e0\u306e\u62e1\u5927: \u65e9\u671f\u8a3a\u65ad\u3068\u65e9\u671f\u6cbb\u7642\u3092\u53ef\u80fd\u306b\u3059\u308b\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u306e\u666e\u53ca\u304c\u3001\u6cbb\u7642\u60a3\u8005\u6570\u306e\u5897\u52a0\u306b\u3064\u306a\u304c\u3063\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u60a3\u8005\u4e2d\u5fc3\u306e\u30c7\u30ea\u30d0\u30ea\u30fc\u3078\u306e\u79fb\u884c: \u60a3\u8005\u306e\u5229\u4fbf\u6027\u3068\u6cbb\u7642\u30a2\u30c9\u30d2\u30a2\u30e9\u30f3\u30b9\u306e\u5411\u4e0a\u3092\u76ee\u6307\u3057\u3001\u5728\u5b85\u533b\u7642\u306a\u3069\u306e\u60a3\u8005\u4e2d\u5fc3\u306e\u30b5\u30fc\u30d3\u30b9\u63d0\u4f9b\u30e2\u30c7\u30eb\u304c\u62e1\u5927\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u9175\u7d20\u5de5\u5b66\u306b\u304a\u3051\u308b\u6280\u8853\u9032\u6b69: \u3088\u308a\u52b9\u679c\u7684\u3067\u5b89\u5168\u306a\u9175\u7d20\u88fd\u5264\u306e\u958b\u767a\u304c\u9032\u3093\u3067\u3044\u307e\u3059\u3002<br \/>\n*   \u9769\u65b0\u7684\u306a\u511f\u9084\u30e2\u30c7\u30eb: \u6cbb\u7642\u8cbb\u306e\u9ad8\u9a30\u306b\u5bfe\u5fdc\u3059\u308b\u305f\u3081\u3001\u6210\u679c\u9023\u52d5\u578b\u3084\u30d0\u30ea\u30e5\u30fc\u30d9\u30fc\u30b9\u306e\u511f\u9084\u30e2\u30c7\u30eb\u304c\u5c0e\u5165\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>4. \u5e02\u5834\u306e\u963b\u5bb3\u8981\u56e0<br \/>\n\u4e00\u65b9\u3067\u3001\u5e02\u5834\u306e\u6210\u9577\u3092\u59a8\u3052\u308b\u8981\u56e0\u3082\u5b58\u5728\u3057\u307e\u3059\u3002<br \/>\n*   \u9ad8\u984d\u306a\u6cbb\u7642\u8cbb: \u9175\u7d20\u88dc\u5145\u7642\u6cd5\u306f\u975e\u5e38\u306b\u9ad8\u984d\u3067\u3042\u308a\u3001\u60a3\u8005\u3084\u533b\u7642\u30b7\u30b9\u30c6\u30e0\u306b\u3068\u3063\u3066\u5927\u304d\u306a\u8ca0\u62c5\u3068\u306a\u3063\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u514d\u75ab\u539f\u6027\u306e\u61f8\u5ff5: \u6295\u4e0e\u3055\u308c\u305f\u9175\u7d20\u306b\u5bfe\u3059\u308b\u514d\u75ab\u53cd\u5fdc\u304c\u3001\u6cbb\u7642\u52b9\u679c\u306e\u4f4e\u4e0b\u3084\u526f\u4f5c\u7528\u3092\u5f15\u304d\u8d77\u3053\u3059\u53ef\u80fd\u6027\u304c\u3042\u308a\u307e\u3059\u3002<br \/>\n*   \u65b0\u8208\u6cbb\u7642\u6cd5\u3068\u306e\u7af6\u5408: \u907a\u4f1d\u5b50\u6cbb\u7642\u3084\u30b7\u30e3\u30da\u30ed\u30f3\u7642\u6cd5\u306a\u3069\u3001\u65b0\u305f\u306a\u6cbb\u7642\u6cd5\u306e\u958b\u767a\u304c\u9032\u3093\u3067\u304a\u308a\u3001\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u3068\u306e\u7af6\u5408\u304c\u4e88\u60f3\u3055\u308c\u307e\u3059\u3002<br \/>\n*   \u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u306e\u8ab2\u984c: \u5e0c\u5c11\u75be\u60a3\u6cbb\u7642\u85ac\u306e\u88fd\u9020\u3068\u4f9b\u7d66\u306b\u306f\u3001\u8907\u96d1\u306a\u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u7ba1\u7406\u304c\u4f34\u3044\u307e\u3059\u3002<\/p>\n<p>5. \u898f\u5236\u74b0\u5883\u3068\u30dd\u30fc\u30bf\u30fc\u306e\u30d5\u30a1\u30a4\u30d6\u30d5\u30a9\u30fc\u30b9\u5206\u6790<br \/>\n\u30ec\u30dd\u30fc\u30c8\u3067\u306f\u3001\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u5e02\u5834\u306b\u304a\u3051\u308b\u898f\u5236\u74b0\u5883\u306e\u73fe\u72b6\u3068\u3001\u30dd\u30fc\u30bf\u30fc\u306e\u30d5\u30a1\u30a4\u30d6\u30d5\u30a9\u30fc\u30b9\u5206\u6790\u3092\u901a\u3058\u3066\u3001\u65b0\u898f\u53c2\u5165\u306e\u8105\u5a01\u3001\u8cb7\u3044\u624b\u306e\u4ea4\u6e09\u529b\u3001\u30b5\u30d7\u30e9\u30a4\u30e4\u30fc\u306e\u4ea4\u6e09\u529b\u3001\u4ee3\u66ff\u54c1\u306e\u8105\u5a01\u3001\u304a\u3088\u3073\u65e2\u5b58\u4f01\u696d\u9593\u306e\u7af6\u4e89\u306e\u6fc0\u3057\u3055\u3068\u3044\u3063\u305f\u7af6\u4e89\u8981\u56e0\u304c\u8a73\u7d30\u306b\u5206\u6790\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>6. \u5e02\u5834\u306e\u30bb\u30b0\u30e1\u30f3\u30c6\u30fc\u30b7\u30e7\u30f3<br \/>\n\u5e02\u5834\u306f\u3001\u4ee5\u4e0b\u306e\u4e3b\u8981\u306a\u30bb\u30b0\u30e1\u30f3\u30c8\u306b\u5206\u985e\u3055\u308c\u3001\u8a73\u7d30\u306a\u5206\u6790\u304c\u884c\u308f\u308c\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u9175\u7d20\u30bf\u30a4\u30d7\u5225: Imiglucerase\u3001Agalsidase Alfa\u3001Agalsidase Beta\u3001Velaglucerase Alfa\u3001Taliglucerase Alfa\u3001Alglucosidase Alfa\u3001Avalglucosidase Alfa\u3001Galsulfase\u3001Idursulfase\u3001\u305d\u306e\u4ed6\u306e\u9175\u7d20\u3002<br \/>\n*   \u7528\u9014\u5225: \u30b4\u30fc\u30b7\u30a7\u75c5\uff08I\u578b\u3001II\u578b\u3001III\u578b\uff09\u3001\u30dd\u30f3\u30da\u75c5\uff08\u4e73\u5150\u578b\u304a\u3088\u3073\u9045\u767a\u578b\uff09\u3001\u30d5\u30a1\u30d6\u30ea\u30fc\u75c5\u3001MPS I\uff08\u30cf\u30fc\u30e9\u30fc\u75c7\u5019\u7fa4\uff09\u3001MPS II\uff08\u30cf\u30f3\u30bf\u30fc\u75c7\u5019\u7fa4\uff09\u3001MPS IV\uff08\u30e2\u30eb\u30ad\u30aa\u75c7\u5019\u7fa4\uff09\u3001\u305d\u306e\u4ed6\u306e\u7528\u9014\u3002<br \/>\n*   \u6295\u4e0e\u7d4c\u8def\u5225: \u9759\u8108\u5185\u6ce8\u5165\u3001\u76ae\u4e0b\u6295\u4e0e\u3002<br \/>\n*   \u88fd\u5264\u5225: \u6a19\u6e96\u7d44\u63db\u3048\u9175\u7d20\u3001PEG\u5316\/\u878d\u5408\u30bf\u30f3\u30d1\u30af\u8cea\u3001\u907a\u4f1d\u5b50\u6d3b\u6027\u5316\u6b21\u4e16\u4ee3\u9175\u7d20\u3002<br \/>\n*   \u30a8\u30f3\u30c9\u30e6\u30fc\u30b6\u30fc\u5225: \u75c5\u9662\u30fb\u5c02\u9580\u30af\u30ea\u30cb\u30c3\u30af\u3001\u5728\u5b85\u533b\u7642\u65bd\u8a2d\u3001\u6ce8\u5165\u30bb\u30f3\u30bf\u30fc\u3002<br \/>\n*   \u5730\u57df\u5225: \u5317\u7c73\uff08\u7c73\u56fd\u3001\u30ab\u30ca\u30c0\u3001\u30e1\u30ad\u30b7\u30b3\uff09\u3001\u6b27\u5dde\uff08\u30c9\u30a4\u30c4\u3001\u82f1\u56fd\u3001\u30d5\u30e9\u30f3\u30b9\u3001\u30a4\u30bf\u30ea\u30a2\u3001\u30b9\u30da\u30a4\u30f3\u3001\u305d\u306e\u4ed6\u306e\u6b27\u5dde\uff09\u3001\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\uff08\u4e2d\u56fd\u3001\u65e5\u672c\u3001\u30a4\u30f3\u30c9\u3001\u30aa\u30fc\u30b9\u30c8\u30e9\u30ea\u30a2\u3001\u97d3\u56fd\u3001\u305d\u306e\u4ed6\u306e\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\uff09\u3001\u4e2d\u6771\u30fb\u30a2\u30d5\u30ea\u30ab\uff08GCC\u3001\u5357\u30a2\u30d5\u30ea\u30ab\u3001\u305d\u306e\u4ed6\u306e\u4e2d\u6771\u30fb\u30a2\u30d5\u30ea\u30ab\uff09\u3001\u5357\u7c73\uff08\u30d6\u30e9\u30b8\u30eb\u3001\u30a2\u30eb\u30bc\u30f3\u30c1\u30f3\u3001\u305d\u306e\u4ed6\u306e\u5357\u7c73\uff09\u3002<\/p>\n<p>7. \u7af6\u4e89\u74b0\u5883<br \/>\n\u5e02\u5834\u96c6\u4e2d\u5ea6\u3068\u5e02\u5834\u30b7\u30a7\u30a2\u5206\u6790\u3092\u901a\u3058\u3066\u3001\u7af6\u4e89\u74b0\u5883\u304c\u8a55\u4fa1\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u4e3b\u8981\u306a\u7af6\u5408\u4f01\u696d\u3068\u3057\u3066\u306f\u3001Sanofi (Genzyme)\u3001Takeda Pharmaceutical Co. Ltd\u3001BioMarin Pharmaceutical Inc.\u3001Amicus Therapeutics\u3001Ultragenyx Pharmaceutical Inc.\u3001Spark Therapeutics\u3001JCR Pharmaceuticals Co. Ltd.\u3001Protalix Biotherapeutics\u3001Chiesi Farmaceutici S.p.A.\u3001GC Pharma (Green Cross Corp.)\u3001ISU Abxis\u3001Denali Therapeutics\u3001CANbridge Pharmaceuticals Inc.\u3001Pharming Group N.V.\u3001SOBI (Orphan Biovitrum)\u3001Avacta Group plc\u3001Orchard Therapeutics\u3001EUSA Pharma\u3001Idorsia Pharmaceuticals\u306a\u3069\u304c\u6319\u3052\u3089\u308c\u3001\u5404\u793e\u306e\u30b0\u30ed\u30fc\u30d0\u30eb\u304a\u3088\u3073\u5e02\u5834\u30ec\u30d9\u30eb\u306e\u6982\u8981\u3001\u4e3b\u8981\u4e8b\u696d\u30bb\u30b0\u30e1\u30f3\u30c8\u3001\u8ca1\u52d9\u72b6\u6cc1\u3001\u5f93\u696d\u54e1\u6570\u3001\u4e3b\u8981\u60c5\u5831\u3001\u5e02\u5834\u30e9\u30f3\u30af\u3001\u5e02\u5834\u30b7\u30a7\u30a2\u3001\u88fd\u54c1\u3068\u30b5\u30fc\u30d3\u30b9\u3001\u304a\u3088\u3073\u6700\u8fd1\u306e\u52d5\u5411\u304c\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>8. \u5e02\u5834\u306e\u6a5f\u4f1a\u3068\u5c06\u6765\u5c55\u671b<br \/>\n\u30ec\u30dd\u30fc\u30c8\u3067\u306f\u3001\u672a\u958b\u62d3\u9818\u57df\u3068\u6e80\u305f\u3055\u308c\u3066\u3044\u306a\u3044\u30cb\u30fc\u30ba\u306e\u8a55\u4fa1\u3092\u901a\u3058\u3066\u3001\u9175\u7d20\u88dc\u5145\u7642\u6cd5\u5e02\u5834\u306b\u304a\u3051\u308b\u5c06\u6765\u306e\u6210\u9577\u6a5f\u4f1a\u304c\u7279\u5b9a\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>9. \u8abf\u67fb\u65b9\u6cd5\u8ad6\u306e\u4fe1\u983c\u6027<br \/>\nMordor Intelligence\u306e\u8abf\u67fb\u306f\u3001\u305d\u306e\u4fe1\u983c\u6027\u306b\u5f37\u307f\u3092\u6301\u3063\u3066\u3044\u307e\u3059\u3002\u4e00\u6b21\u8abf\u67fb\u3068\u3057\u3066\u3001\u5317\u7c73\u3001\u6b27\u5dde\u3001\u30a2\u30b8\u30a2\u306e\u81e8\u5e8a\u907a\u4f1d\u5b66\u8005\u3001\u6ce8\u5165\u30bb\u30f3\u30bf\u30fc\u306e\u85ac\u5264\u5e2b\u3001\u5e0c\u5c11\u75be\u60a3\u64c1\u8b77\u8005\u3078\u306e\u30a4\u30f3\u30bf\u30d3\u30e5\u30fc\u3084\u30a2\u30f3\u30b1\u30fc\u30c8\u3092\u5b9f\u65bd\u3057\u3001\u6cbb\u7642\u60a3\u8005\u30d7\u30fc\u30eb\u3001\u6295\u4e0e\u9075\u5b88\u3001\u5728\u5b85\u6ce8\u5165\u30b5\u30fc\u30d3\u30b9\u3078\u306e\u79fb\u884c\u306b\u95a2\u3059\u308b\u4eee\u5b9a\u3092\u691c\u8a3c\u3057\u3066\u3044\u307e\u3059\u3002\u4e8c\u6b21\u8abf\u67fb\u3067\u306f\u3001\u56fd\u7acb\u885b\u751f\u7814\u7a76\u6240\u306e\u907a\u4f1d\u6027\u5e0c\u5c11\u75be\u60a3\uff08GARD\uff09\u30d7\u30ed\u30b0\u30e9\u30e0\u3001EuroDIS\u3001\u65e5\u672c\u306eNCNP\u3001Pan-Canadian Pharmaceutical Alliance\u306a\u3069\u306e\u516c\u7684\u767b\u9332\u3001\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u30c0\u30c3\u30b7\u30e5\u30dc\u30fc\u30c9\u3001\u511f\u9084\u30b9\u30b1\u30b8\u30e5\u30fc\u30eb\u3092\u5206\u6790\u3057\u3066\u3044\u307e\u3059\u3002\u4f01\u696d\u5831\u544a\u66f8\u3084\u79d1\u5b66\u96d1\u8a8c\u3082\u6d3b\u7528\u3057\u3001D&#038;B Hoovers\u3084Dow Jones Factiva\u306e\u3088\u3046\u306a\u6709\u6599\u30c7\u30fc\u30bf\u30bb\u30c3\u30c8\u3082\u53c2\u7167\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n\u5e02\u5834\u898f\u6a21\u306e\u4e88\u6e2c\u306f\u3001\u6709\u75c5\u7387\u304b\u3089\u6cbb\u7642\u60a3\u8005\u3078\u306e\u30c8\u30c3\u30d7\u30c0\u30a6\u30f3\u30a2\u30d7\u30ed\u30fc\u30c1\u3092\u57fa\u672c\u3068\u3057\u3001\u56fd\u306e\u767b\u9332\u6570\u3001\u6cbb\u7642\u6cd5\u306e\u666e\u53ca\u7387\u3001\u60a3\u8005\u3042\u305f\u308a\u306e\u5e74\u9593\u5e73\u5747\u8cbb\u7528\u3067\u8abf\u6574\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u307e\u305f\u3001\u30b5\u30d7\u30e9\u30a4\u30e4\u30fc\u306e\u51fa\u8377\u91cf\u3084\u9078\u629e\u7684\u306a\u30c1\u30e3\u30cd\u30eb\u30c1\u30a7\u30c3\u30af\u306b\u3088\u308b\u30dc\u30c8\u30e0\u30a2\u30c3\u30d7\u691c\u8a3c\u3082\u884c\u308f\u308c\u3066\u3044\u307e\u3059\u3002\u4e3b\u8981\u5909\u6570\u306b\u306f\u3001\u8a3a\u65ad\u3055\u308c\u305f\u6709\u75c5\u7387\u306e\u6210\u9577\u3001\u6cbb\u7642\u3078\u306e\u8ee2\u63db\u7387\u3001\u5e73\u5747\u8ca9\u58f2\u4fa1\u683c\uff08ASP\uff09\u306e\u63a8\u79fb\u3001\u511f\u9084\u306e\u8abf\u6574\u3001\u6ce8\u5165\u30b5\u30a4\u30c8\u306e\u69cb\u6210\u306a\u3069\u304c\u542b\u307e\u308c\u3001ARIMA\u6642\u7cfb\u5217\u5e73\u6ed1\u5316\u3068\u30b7\u30ca\u30ea\u30aa\u5206\u6790\u3092\u901a\u3058\u30662030\u5e74\u307e\u3067\u306e\u53ce\u76ca\u304c\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002<br 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