{"id":90454,"date":"2026-01-08T06:31:49","date_gmt":"2026-01-07T21:31:49","guid":{"rendered":"https:\/\/www.marketresearch.co.jp\/insights\/amyotrophic-lateral-sclerosis-treatment-market-mordor\/"},"modified":"2026-04-03T06:19:48","modified_gmt":"2026-04-02T21:19:48","slug":"amyotrophic-lateral-sclerosis-treatment-market-mordor","status":"publish","type":"post","link":"https:\/\/www.marketresearch.co.jp\/insights\/amyotrophic-lateral-sclerosis-treatment-market-mordor\/","title":{"rendered":"\u7b4b\u840e\u7e2e\u6027\u5074\u7d22\u786c\u5316\u75c7\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u30fb\u30b7\u30a7\u30a2\u5206\u6790 &#8211; \u6210\u9577\u30c8\u30ec\u30f3\u30c9\u30fb\u4e88\u6e2c (2025-2030\u5e74)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.marketresearch.co.jp\/insights\/wp-content\/uploads\/2026\/01\/amyotrophic-lateral-sclerosis-treatment-market-1729078553019-MI-Logo-and-CL-Template.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.marketresearch.co.jp\/insights\/wp-content\/uploads\/2026\/01\/1735907811620-amyotrophic-lateral-sclerosis-treatment-market-Market-Summary.png\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \u306f\u3058\u3081\u306b<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \u8abf\u67fb\u306e\u524d\u63d0\u3068\u5e02\u5834\u306e\u5b9a\u7fa9<\/li>\n<li class=\"toc-level-2\">1.2 \u8abf\u67fb\u7bc4\u56f2<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \u8abf\u67fb\u65b9\u6cd5<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \u30a8\u30b0\u30bc\u30af\u30c6\u30a3\u30d6\u30b5\u30de\u30ea\u30fc<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \u5e02\u5834\u6982\u6cc1<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \u5e02\u5834\u6982\u8981<\/li>\n<li class=\"toc-level-2\">4.2 \u5e02\u5834\u306e\u63a8\u9032\u8981\u56e0\n<ul>\n<li class=\"toc-level-3\">4.2.1 ALS\u306e\u767a\u751f\u7387\u3068\u6709\u75c5\u7387\u306e\u5897\u52a0<\/li>\n<li class=\"toc-level-3\">4.2.2 \u5e0c\u5c11\u75be\u75c5\u7528\u533b\u85ac\u54c1\u306b\u5bfe\u3059\u308b\u898f\u5236\u4e0a\u306e\u8ffd\u3044\u98a8<\/li>\n<li class=\"toc-level-3\">4.2.3 \u907a\u4f1d\u5b50\u6cbb\u7642\u304a\u3088\u3073\u30a2\u30f3\u30c1\u30bb\u30f3\u30b9\u30aa\u30ea\u30b4\u30cc\u30af\u30ec\u30aa\u30c1\u30c9\u6cbb\u7642\u306b\u304a\u3051\u308b\u30d6\u30ec\u30fc\u30af\u30b9\u30eb\u30fc<\/li>\n<li class=\"toc-level-3\">4.2.4 AI\u4e3b\u5c0e\u306e\u85ac\u5264\u518d\u5229\u7528\u306b\u3088\u308b\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u306e\u591a\u69d8\u5316\u306e\u52a0\u901f<\/li>\n<li class=\"toc-level-3\">4.2.5 \u6cbb\u9a13\u85ac\u30a2\u30af\u30bb\u30b9\u6cd5\u3068\u62e1\u5927\u30a2\u30af\u30bb\u30b9\u6cd5\u306b\u3088\u308b\u65e9\u671f\u5c0e\u5165\u306e\u4fc3\u9032<\/li>\n<li class=\"toc-level-3\">4.2.6 \u30c7\u30b8\u30bf\u30eb\u30d0\u30a4\u30aa\u30de\u30fc\u30ab\u30fc\u3068\u9060\u9694\u60a3\u8005\u30e2\u30cb\u30bf\u30ea\u30f3\u30b0\u306e\u63a1\u7528<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \u5e02\u5834\u306e\u963b\u5bb3\u8981\u56e0\n<ul>\n<li class=\"toc-level-3\">4.3.1 \u9ad8\u984d\u306a\u6cbb\u7642\u8cbb\u3068\u9650\u3089\u308c\u305f\u511f\u9084<\/li>\n<li class=\"toc-level-3\">4.3.2 \u73fe\u5728\u306e\u75be\u60a3\u4fee\u98fe\u85ac\u306e\u9650\u3089\u308c\u305f\u6709\u52b9\u6027<\/li>\n<li class=\"toc-level-3\">4.3.3 \u751f\u7269\u88fd\u5264\/\u81ea\u5df1\u7d30\u80deCMC\u306e\u751f\u7523\u80fd\u529b\u306e\u30dc\u30c8\u30eb\u30cd\u30c3\u30af<\/li>\n<li class=\"toc-level-3\">4.3.4 \u9577\u671f\u30a8\u30c0\u30e9\u30dc\u30f3\u4f7f\u7528\u306b\u304a\u3051\u308b\u65b0\u305f\u306a\u5b89\u5168\u6027\u30b7\u30b0\u30ca\u30eb<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u5206\u6790<\/li>\n<li class=\"toc-level-2\">4.5 \u898f\u5236\u74b0\u5883<\/li>\n<li class=\"toc-level-2\">4.6 \u6280\u8853\u7684\u5c55\u671b<\/li>\n<li class=\"toc-level-2\">4.7 \u30dd\u30fc\u30bf\u30fc\u306e5\u3064\u306e\u529b\u5206\u6790\n<ul>\n<li class=\"toc-level-3\">4.7.1 \u65b0\u898f\u53c2\u5165\u306e\u8105\u5a01<\/li>\n<li class=\"toc-level-3\">4.7.2 \u8cb7\u3044\u624b\u306e\u4ea4\u6e09\u529b<\/li>\n<li class=\"toc-level-3\">4.7.3 \u4f9b\u7d66\u8005\u306e\u4ea4\u6e09\u529b<\/li>\n<li class=\"toc-level-3\">4.7.4 \u4ee3\u66ff\u54c1\u306e\u8105\u5a01<\/li>\n<li class=\"toc-level-3\">4.7.5 \u7af6\u4e89\u306e\u6fc0\u3057\u3055<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \u5e02\u5834\u898f\u6a21\u3068\u6210\u9577\u4e88\u6e2c\uff08\u91d1\u984d\u3001\u7c73\u30c9\u30eb\uff09<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \u6cbb\u7642\u30bf\u30a4\u30d7\u5225\n<ul>\n<li class=\"toc-level-3\">5.1.1 \u6295\u85ac<\/li>\n<li class=\"toc-level-3\">5.1.2 \u5e79\u7d30\u80de\u6cbb\u7642<\/li>\n<li class=\"toc-level-3\">5.1.3 \u907a\u4f1d\u5b50\/ASO\u6cbb\u7642<\/li>\n<li class=\"toc-level-3\">5.1.4 \u305d\u306e\u4ed6<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \u85ac\u5264\u30af\u30e9\u30b9\u5225\n<ul>\n<li class=\"toc-level-3\">5.2.1 \u30ea\u30eb\u30be\u30fc\u30eb<\/li>\n<li class=\"toc-level-3\">5.2.2 \u30a8\u30c0\u30e9\u30dc\u30f3<\/li>\n<li class=\"toc-level-3\">5.2.3 \u30a2\u30f3\u30c1\u30bb\u30f3\u30b9\u30aa\u30ea\u30b4\u30cc\u30af\u30ec\u30aa\u30c1\u30c9<\/li>\n<li class=\"toc-level-3\">5.2.4 \u4f75\u7528\/\u591a\u6a19\u7684<\/li>\n<li class=\"toc-level-3\">5.2.5 \u5bfe\u75c7\u7642\u6cd5\u85ac<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \u6295\u4e0e\u7d4c\u8def\u5225\n<ul>\n<li class=\"toc-level-3\">5.3.1 \u7d4c\u53e3<\/li>\n<li class=\"toc-level-3\">5.3.2 \u9759\u8108\u5185<\/li>\n<li class=\"toc-level-3\">5.3.3 \u9ac4\u8154\u5185<\/li>\n<li class=\"toc-level-3\">5.3.4 \u76ae\u4e0b<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.4 \u30a8\u30f3\u30c9\u30e6\u30fc\u30b6\u30fc\u5225\n<ul>\n<li class=\"toc-level-3\">5.4.1 \u75c5\u9662<\/li>\n<li class=\"toc-level-3\">5.4.2 \u5c02\u9580\u30af\u30ea\u30cb\u30c3\u30af\/ALS\u30bb\u30f3\u30bf\u30fc<\/li>\n<li class=\"toc-level-3\">5.4.3 \u5728\u5b85\u533b\u7642\u65bd\u8a2d<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.5 \u6d41\u901a\u30c1\u30e3\u30cd\u30eb\u5225\n<ul>\n<li class=\"toc-level-3\">5.5.1 \u75c5\u9662\u85ac\u5c40<\/li>\n<li class=\"toc-level-3\">5.5.2 \u5c0f\u58f2\u85ac\u5c40<\/li>\n<li class=\"toc-level-3\">5.5.3 \u30aa\u30f3\u30e9\u30a4\u30f3\u85ac\u5c40<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.6 \u5730\u57df\u5225\n<ul>\n<li class=\"toc-level-3\">5.6.1 \u5317\u7c73<\/li>\n<li class=\"toc-level-4\">5.6.1.1 \u7c73\u56fd<\/li>\n<li class=\"toc-level-4\">5.6.1.2 \u30ab\u30ca\u30c0<\/li>\n<li class=\"toc-level-4\">5.6.1.3 \u30e1\u30ad\u30b7\u30b3<\/li>\n<li class=\"toc-level-3\">5.6.2 \u30e8\u30fc\u30ed\u30c3\u30d1<\/li>\n<li class=\"toc-level-4\">5.6.2.1 \u30c9\u30a4\u30c4<\/li>\n<li class=\"toc-level-4\">5.6.2.2 \u30a4\u30ae\u30ea\u30b9<\/li>\n<li class=\"toc-level-4\">5.6.2.3 \u30d5\u30e9\u30f3\u30b9<\/li>\n<li class=\"toc-level-4\">5.6.2.4 \u30a4\u30bf\u30ea\u30a2<\/li>\n<li class=\"toc-level-4\">5.6.2.5 \u30b9\u30da\u30a4\u30f3<\/li>\n<li class=\"toc-level-4\">5.6.2.6 \u305d\u306e\u4ed6\u306e\u30e8\u30fc\u30ed\u30c3\u30d1<\/li>\n<li class=\"toc-level-3\">5.6.3 \u30a2\u30b8\u30a2\u592a\u5e73\u6d0b<\/li>\n<li class=\"toc-level-4\">5.6.3.1 \u4e2d\u56fd<\/li>\n<li class=\"toc-level-4\">5.6.3.2 \u65e5\u672c<\/li>\n<li class=\"toc-level-4\">5.6.3.3 \u30a4\u30f3\u30c9<\/li>\n<li class=\"toc-level-4\">5.6.3.4 \u97d3\u56fd<\/li>\n<li class=\"toc-level-4\">5.6.3.5 \u30aa\u30fc\u30b9\u30c8\u30e9\u30ea\u30a2<\/li>\n<li class=\"toc-level-4\">5.6.3.6 \u305d\u306e\u4ed6\u306e\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b<\/li>\n<li class=\"toc-level-3\">5.6.4 \u4e2d\u6771\u30fb\u30a2\u30d5\u30ea\u30ab<\/li>\n<li class=\"toc-level-4\">5.6.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.6.4.2 \u5357\u30a2\u30d5\u30ea\u30ab<\/li>\n<li class=\"toc-level-4\">5.6.4.3 \u305d\u306e\u4ed6\u306e\u4e2d\u6771\u30fb\u30a2\u30d5\u30ea\u30ab<\/li>\n<li class=\"toc-level-3\">5.6.5 \u5357\u7c73<\/li>\n<li class=\"toc-level-4\">5.6.5.1 \u30d6\u30e9\u30b8\u30eb<\/li>\n<li class=\"toc-level-4\">5.6.5.2 \u30a2\u30eb\u30bc\u30f3\u30c1\u30f3<\/li>\n<li class=\"toc-level-4\">5.6.5.3 \u305d\u306e\u4ed6\u306e\u5357\u7c73<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \u7af6\u5408\u60c5\u52e2<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \u5e02\u5834\u96c6\u4e2d\u5ea6<\/li>\n<li class=\"toc-level-2\">6.2 \u5e02\u5834\u30b7\u30a7\u30a2\u5206\u6790<\/li>\n<li class=\"toc-level-2\">6.3 \u4f01\u696d\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\uff08\u30b0\u30ed\u30fc\u30d0\u30eb\u6982\u8981\u3001\u5e02\u5834\u6982\u8981\u3001\u4e3b\u8981\u30bb\u30b0\u30e1\u30f3\u30c8\u3001\u8ca1\u52d9\u3001\u6226\u7565\u60c5\u5831\u3001\u5e02\u5834\u30e9\u30f3\u30af\/\u30b7\u30a7\u30a2\u3001\u88fd\u54c1\u30fb\u30b5\u30fc\u30d3\u30b9\u3001\u6700\u8fd1\u306e\u52d5\u5411\u3092\u542b\u3080\uff09\n<ul>\n<li class=\"toc-level-3\">6.3.1 \u7530\u8fba\u4e09\u83f1\u88fd\u85ac\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.2 \u30a8\u30a4\u30df\u30ec\u30c3\u30af\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.3 \u30b5\u30f3\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30fb\u30a4\u30f3\u30c0\u30b9\u30c8\u30ea\u30fc\u30ba\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.4 \u30d0\u30a4\u30aa\u30b8\u30a7\u30f3\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.5 \u30a2\u30a4\u30aa\u30cb\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.6 \u30d6\u30ec\u30a4\u30f3\u30b9\u30c8\u30fc\u30e0\u30fb\u30bb\u30eb\u30fb\u30bb\u30e9\u30d4\u30e5\u30fc\u30c6\u30a3\u30af\u30b9\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.7 \u30b3\u30a2\u30b9\u30c6\u30e0\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.8 AB\u30b5\u30a4\u30a8\u30f3\u30b9SA<\/li>\n<li class=\"toc-level-3\">6.3.9 \u30d9\u30fc\u30ea\u30f3\u30ac\u30fc\u30a4\u30f3\u30b2\u30eb\u30cf\u30a4\u30e0\u30fb\u30a4\u30f3\u30bf\u30fc\u30ca\u30b7\u30e7\u30ca\u30ebGmbH<\/li>\n<li class=\"toc-level-3\">6.3.10 \u30a2\u30cd\u30af\u30bd\u30f3\u30fb\u30d0\u30a4\u30aa\u30b5\u30a4\u30a8\u30f3\u30b9\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.11 CRISPR\u30bb\u30e9\u30d4\u30e5\u30fc\u30c6\u30a3\u30af\u30b9AG<\/li>\n<li class=\"toc-level-3\">6.3.12 \u30d0\u30a4\u30aa\u30d8\u30a4\u30d6\u30f3\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.13 \u30b5\u30a4\u30c8\u30ad\u30cd\u30c6\u30a3\u30af\u30b9\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.14 \u30af\u30a2\u30ea\u30b9\u30fb\u30b3\u30fc\u30dd\u30ec\u30fc\u30b7\u30e7\u30f3<\/li>\n<li class=\"toc-level-3\">6.3.15 \u30e1\u30c7\u30a3\u30b7\u30ce\u30d0\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.16 \u6b66\u7530\u85ac\u54c1\u5de5\u696d\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.17 \u30cb\u30e5\u30fc\u30d3\u30dc\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.18 \u30a2\u30b3\u30fc\u30c0\u30fb\u30bb\u30e9\u30d4\u30e5\u30fc\u30c6\u30a3\u30af\u30b9\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.19 \u30b5\u30a4\u30af\u30ec\u30ea\u30aa\u30f3\u30fb\u30bb\u30e9\u30d4\u30e5\u30fc\u30c6\u30a3\u30af\u30b9\u682a\u5f0f\u4f1a\u793e<\/li>\n<li class=\"toc-level-3\">6.3.20 ALS\u30d0\u30a4\u30aa\u30d5\u30a1\u30fc\u30deLLC<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \u5e02\u5834\u6a5f\u4f1a\u3068\u5c06\u6765\u5c55\u671b<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u7b4b\u840e\u7e2e\u6027\u5074\u7d22\u786c\u5316\u75c7\uff08ALS\uff09\u6cbb\u7642\u5e02\u5834\u306e\u6982\u8981\u3092\u4ee5\u4e0b\u306b\u307e\u3068\u3081\u307e\u3059\u3002<\/p>\n<p>&#8212;<\/p>\n<p># \u7b4b\u840e\u7e2e\u6027\u5074\u7d22\u786c\u5316\u75c7\uff08ALS\uff09\u6cbb\u7642\u5e02\u5834\u6982\u8981<\/p>\n<p>\u7b4b\u840e\u7e2e\u6027\u5074\u7d22\u786c\u5316\u75c7\uff08ALS\uff09\u6cbb\u7642\u5e02\u5834\u306f\u30012025\u5e74\u306b\u306f0.9\u5104\u7c73\u30c9\u30eb\u3068\u8a55\u4fa1\u3055\u308c\u30012030\u5e74\u307e\u3067\u306b1.21\u5104\u7c73\u30c9\u30eb\u306b\u9054\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u304a\u308a\u3001\u4e88\u6e2c\u671f\u9593\u4e2d\u306e\u5e74\u5e73\u5747\u6210\u9577\u7387\uff08CAGR\uff09\u306f5.94%\u3092\u8a18\u9332\u3059\u308b\u898b\u8fbc\u307f\u3067\u3059\u3002\u3053\u306e\u6210\u9577\u306f\u3001\u5bfe\u75c7\u7642\u6cd5\u304b\u3089\u75be\u60a3\u4fee\u98fe\u7642\u6cd5\u3078\u306e\u6c7a\u5b9a\u7684\u306a\u8ee2\u63db\u3092\u53cd\u6620\u3057\u3066\u304a\u308a\u3001\u7279\u306b2023\u5e74\u306e\u7c73\u56fd\u3067\u306eSOD1-ALS\u5411\u3051\u521d\u306e\u30a2\u30f3\u30c1\u30bb\u30f3\u30b9\u30aa\u30ea\u30b4\u30cc\u30af\u30ec\u30aa\u30c1\u30c9\uff08ASO\uff09\u306e\u627f\u8a8d\u3001\u305d\u308c\u306b\u7d9a\u304f2024\u5e74\u306e\u6b27\u5dde\u3067\u306e\u627f\u8a8d\u304c\u5e02\u5834\u3092\u727d\u5f15\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u5e02\u5834\u306e\u52e2\u3044\u306f\u3001\u30aa\u30fc\u30d5\u30a1\u30f3\u30c9\u30e9\u30c3\u30b0\u306e\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u306e\u62e1\u5927\u3001\u898f\u5236\u624b\u6570\u6599\u306e\u514d\u9664\u3001\u304a\u3088\u3073\u300cRight-To-Try\u300d\u898f\u5b9a\u306b\u3088\u3063\u3066\u5f37\u5316\u3055\u308c\u3066\u304a\u308a\u3001\u3053\u308c\u3089\u304c\u5e02\u5834\u6295\u5165\u307e\u3067\u306e\u671f\u9593\u3092\u77ed\u7e2e\u3057\u3001\u60a3\u8005\u30a2\u30af\u30bb\u30b9\u3092\u62e1\u5927\u3057\u3066\u3044\u307e\u3059\u3002\u30aa\u30ea\u30b4\u30cc\u30af\u30ec\u30aa\u30c1\u30c9\u88fd\u9020\u306b\u304a\u3051\u308b\u8a2d\u5099\u6295\u8cc7\u3068\u30b9\u30b1\u30fc\u30e9\u30d6\u30eb\u306a\u30a6\u30a4\u30eb\u30b9\u30d9\u30af\u30bf\u30fc\u30d7\u30e9\u30c3\u30c8\u30d5\u30a9\u30fc\u30e0\u306f\u30011\u56de\u3042\u305f\u308a\u306e\u751f\u7523\u30b3\u30b9\u30c8\u3092\u524a\u6e1b\u3057\u3001\u907a\u4f1d\u5b50\u30d9\u30fc\u30b9\u88fd\u54c1\u306e\u7c97\u5229\u76ca\u3092\u6539\u5584\u3057\u3066\u3044\u307e\u3059\u3002\u307e\u305f\u3001\u591a\u5206\u91ce\u9023\u643a\u306eALS\u30bb\u30f3\u30bf\u30fc\u306f\u3001\u751f\u5b58\u7387\u3068\u751f\u6d3b\u306e\u8cea\u306e\u5411\u4e0a\u306b\u8ca2\u732e\u3057\u3066\u304a\u308a\u3001\u5c02\u9580\u30af\u30ea\u30cb\u30c3\u30af\u3067\u306e\u51e6\u65b9\u7b8b\u306e\u7740\u5b9f\u306a\u5897\u52a0\u3092\u652f\u3048\u3066\u3044\u307e\u3059\u3002\u4e00\u65b9\u3067\u3001\u30d0\u30a4\u30aa\u533b\u85ac\u54c1\u306e\u88fd\u9020\u80fd\u529b\u4e0d\u8db3\u3001\u9ad8\u984d\u306a\u6cbb\u7642\u8cbb\u3001\u30a8\u30c0\u30e9\u30dc\u30f3\u306b\u95a2\u3059\u308b\u65b0\u305f\u306a\u5b89\u5168\u6027\u30b7\u30b0\u30ca\u30eb\u3068\u3044\u3063\u305f\u5e02\u5834\u30ea\u30b9\u30af\u3082\u5b58\u5728\u3057\u307e\u3059\u304c\u3001\u60a3\u8005\u652f\u63f4\u56e3\u4f53\u3084AI\u3092\u6d3b\u7528\u3057\u305f\u30c9\u30e9\u30c3\u30b0\u30ea\u30d1\u30fc\u30d1\u30b7\u30f3\u30b0\u306e\u53d6\u308a\u7d44\u307f\u304c\u8cc7\u672c\u6d41\u5165\u3092\u7dad\u6301\u3057\u3001\u6cbb\u7642\u30dd\u30fc\u30c8\u30d5\u30a9\u30ea\u30aa\u3092\u591a\u69d8\u5316\u3055\u305b\u3066\u3044\u307e\u3059\u3002<\/p>\n<p> \u4e3b\u8981\u306a\u30ec\u30dd\u30fc\u30c8\u306e\u30dd\u30a4\u30f3\u30c8<\/p>\n<p>*   \u6cbb\u7642\u30bf\u30a4\u30d7\u5225: 2024\u5e74\u306e\u53ce\u76ca\u3067\u306f\u85ac\u5264\u304c67.2%\u3092\u5360\u3081\u4e3b\u5c0e\u7684\u5730\u4f4d\u306b\u3042\u308a\u307e\u3059\u304c\u3001\u907a\u4f1d\u5b50\u30fbASO\u7642\u6cd5\u306f2030\u5e74\u307e\u3067\u306b6.8%\u306eCAGR\u3067\u62e1\u5927\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u85ac\u5264\u30af\u30e9\u30b9\u5225: 2024\u5e74\u306eALS\u6cbb\u7642\u5e02\u5834\u30b7\u30a7\u30a2\u3067\u306f\u30ea\u30eb\u30be\u30fc\u30eb\u304c38.1%\u3067\u30c8\u30c3\u30d7\u3067\u3057\u305f\u304c\u3001ASO\u306f2030\u5e74\u307e\u3067\u306b5.6%\u306eCAGR\u3067\u6700\u3082\u901f\u3044\u6210\u9577\u3092\u9042\u3052\u308b\u3068\u898b\u8fbc\u307e\u308c\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u6295\u4e0e\u7d4c\u8def\u5225: 2024\u5e74\u306eALS\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3067\u306f\u7d4c\u53e3\u88fd\u54c1\u304c48.2%\u3092\u5360\u3081\u307e\u3057\u305f\u304c\u3001\u9ac4\u8154\u5185\u6295\u4e0e\u306f5.8%\u306eCAGR\u3067\u5897\u52a0\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u30a8\u30f3\u30c9\u30e6\u30fc\u30b6\u30fc\u5225: 2024\u5e74\u306e\u53ce\u76ca\u30b7\u30a7\u30a2\u3067\u306f\u75c5\u9662\u304c64.3%\u3067\u512a\u52e2\u3067\u3057\u305f\u304c\u3001\u5c02\u9580\u30af\u30ea\u30cb\u30c3\u30af\u306f2030\u5e74\u307e\u3067\u306b4.4%\u306eCAGR\u3067\u6700\u3082\u9ad8\u3044\u6210\u9577\u3092\u8a18\u9332\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u5730\u57df\u5225: 2024\u5e74\u306e\u53ce\u76ca\u3067\u306f\u5317\u7c73\u304c42.40%\u3092\u5360\u3081\u307e\u3057\u305f\u304c\u3001\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\u5730\u57df\u306f2030\u5e74\u307e\u3067\u306b7.2%\u306eCAGR\u3067\u6700\u3082\u6025\u901f\u306b\u6210\u9577\u3059\u308b\u3068\u898b\u8fbc\u307e\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p> \u5e02\u5834\u306e\u30c8\u30ec\u30f3\u30c9\u3068\u6d1e\u5bdf<\/p>\n<p>\u4fc3\u9032\u8981\u56e0:<\/p>\n<p>*   ALS\u306e\u767a\u751f\u7387\u3068\u6709\u75c5\u7387\u306e\u5897\u52a0: \u7279\u306b\u9ad8\u9f62\u5316\u304c\u9032\u3080\u6b27\u7c73\u8af8\u56fd\u3067ALS\u306e\u767a\u751f\u7387\u304c\u4e0a\u6607\u3057\u3066\u304a\u308a\u3001\u795e\u7d4c\u8a3a\u65ad\u30c4\u30fc\u30eb\u306e\u9032\u6b69\u306b\u3088\u308a\u8a3a\u65ad\u9045\u5ef6\u304c\u77ed\u7e2e\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u65e9\u671f\u767a\u898b\u306fASO\u306e\u6cbb\u7642\u6a5f\u4f1a\u3092\u5e83\u3052\u3001\u30d7\u30ec\u30df\u30a2\u30e0\u4fa1\u683c\u3092\u652f\u3048\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u30aa\u30fc\u30d5\u30a1\u30f3\u30c9\u30e9\u30c3\u30b0\/\u5e0c\u5c11\u75be\u60a3\u85ac\u306b\u5bfe\u3059\u308b\u898f\u5236\u4e0a\u306e\u8ffd\u3044\u98a8: FDA\u306b\u3088\u308b\u30c8\u30d5\u30a7\u30eb\u30bb\u30f3\u306e\u8fc5\u901f\u627f\u8a8d\u3084EMA\u306b\u3088\u308b\u7279\u4f8b\u627f\u8a8d\u306f\u3001\u8fc5\u901f\u3067\u30a8\u30d3\u30c7\u30f3\u30b9\u9069\u5fdc\u578b\u306e\u5be9\u67fb\u3078\u306e\u8ee2\u63db\u3092\u793a\u3057\u3066\u3044\u307e\u3059\u3002\u624b\u6570\u6599\u514d\u9664\u3001\u512a\u5148\u5be9\u67fb\u30d0\u30a6\u30c1\u30e3\u30fc\u3001\u72ec\u5360\u671f\u9593\u5ef6\u9577\u306a\u3069\u306e\u30a4\u30f3\u30bb\u30f3\u30c6\u30a3\u30d6\u304c\u958b\u767a\u671f\u9593\u3092\u77ed\u7e2e\u3057\u3001\u6295\u8cc7\u3092\u547c\u3073\u8fbc\u3093\u3067\u3044\u307e\u3059\u3002<br \/>\n*   \u907a\u4f1d\u5b50\u304a\u3088\u3073\u30a2\u30f3\u30c1\u30bb\u30f3\u30b9\u30aa\u30ea\u30b4\u30cc\u30af\u30ec\u30aa\u30c1\u30c9\uff08ASO\uff09\u7642\u6cd5\u306e\u30d6\u30ec\u30fc\u30af\u30b9\u30eb\u30fc: SOD1\u3092\u6a19\u7684\u3068\u3057\u305fASO\u304c\u795e\u7d4c\u30d5\u30a3\u30e9\u30e1\u30f3\u30c8\u8efd\u9396\u309255%\u6e1b\u5c11\u3055\u305b\u305f\u3068\u3044\u3046\u753b\u671f\u7684\u306a\u7b2c3\u76f8\u8a66\u9a13\u7d50\u679c\u306f\u3001\u30d0\u30a4\u30aa\u30de\u30fc\u30ab\u30fc\u4e3b\u5c0e\u306e\u75be\u60a3\u4fee\u98fe\u3092\u78ba\u8a8d\u3057\u307e\u3057\u305f\u3002\u30d7\u30e9\u30c3\u30c8\u30d5\u30a9\u30fc\u30e0\u306e\u30e2\u30b8\u30e5\u30fc\u30eb\u5316\u306b\u3088\u308a\u3001FUS-ALS\u3084C9orf72-ALS\u5411\u3051\u306e\u5909\u7570\u7279\u7570\u7684\u5019\u88dc\u85ac\u306e\u958b\u767a\u304c\u52a0\u901f\u3057\u3001\u5f37\u56fa\u306a\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u3092\u5f62\u6210\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   AI\u3092\u6d3b\u7528\u3057\u305f\u30c9\u30e9\u30c3\u30b0\u30ea\u30d1\u30fc\u30d1\u30b7\u30f3\u30b0\u306b\u3088\u308b\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u306e\u591a\u69d8\u5316: \u6a5f\u68b0\u5b66\u7fd2\u30a8\u30f3\u30b8\u30f3\u304c\u30de\u30eb\u30c1\u30aa\u30df\u30af\u30b9\u30c7\u30fc\u30bf\u30bb\u30c3\u30c8\u3092\u89e3\u6790\u3057\u3001FB1006\u306e\u3088\u3046\u306a\u30c9\u30e9\u30c3\u30b0\u30ea\u30d1\u30fc\u30d1\u30b7\u30f3\u30b0\u5019\u88dc\u3092\u7279\u5b9a\u3057\u307e\u3057\u305f\u3002\u3053\u308c\u306b\u3088\u308a\u3001\u521d\u671f\u6bb5\u968e\u306eR&#038;D\u8cbb\u7528\u304c\u6700\u592770%\u524a\u6e1b\u3055\u308c\u3001\u708e\u75c7\u3001\u30df\u30c8\u30b3\u30f3\u30c9\u30ea\u30a2\u6a5f\u80fd\u4e0d\u5168\u3001\u30b7\u30ca\u30d7\u30b9\u6a5f\u80fd\u4e0d\u5168\u3092\u6a19\u7684\u3068\u3059\u308b\u4f75\u7528\u7642\u6cd5\u3092\u542b\u3080\u5019\u88dc\u85ac\u306e\u591a\u69d8\u5316\u304c\u9032\u3093\u3067\u3044\u307e\u3059\u3002<br \/>\n*   Right-To-Try\u304a\u3088\u3073\u62e1\u5927\u30a2\u30af\u30bb\u30b9\u6cd5\u306b\u3088\u308b\u65e9\u671f\u5c0e\u5165\u306e\u4fc3\u9032: \u5317\u7c73\u3092\u4e2d\u5fc3\u306b\u3001\u3053\u308c\u3089\u306e\u6cd5\u5f8b\u304c\u60a3\u8005\u306e\u9769\u65b0\u7684\u306a\u6cbb\u7642\u3078\u306e\u65e9\u671f\u30a2\u30af\u30bb\u30b9\u3092\u5f8c\u62bc\u3057\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u30c7\u30b8\u30bf\u30eb\u30d0\u30a4\u30aa\u30de\u30fc\u30ab\u30fc\u3068\u9060\u9694\u60a3\u8005\u30e2\u30cb\u30bf\u30ea\u30f3\u30b0\u306e\u63a1\u7528: \u30c7\u30b8\u30bf\u30eb\u6280\u8853\u306e\u6210\u719f\u3057\u305f\u5e02\u5834\u3092\u4e2d\u5fc3\u306b\u3001\u60a3\u8005\u30e2\u30cb\u30bf\u30ea\u30f3\u30b0\u3068\u30b1\u30a2\u306e\u52b9\u7387\u5316\u304c\u9032\u3093\u3067\u3044\u307e\u3059\u3002<\/p>\n<p>\u6291\u5236\u8981\u56e0:<\/p>\n<p>*   \u9ad8\u984d\u306a\u6cbb\u7642\u8cbb\u3068\u9650\u3089\u308c\u305f\u511f\u9084: \u627f\u8a8d\u3055\u308c\u305fASO\u306e\u5e74\u9593\u6cbb\u7642\u8cbb\u306f45\u4e07\u7c73\u30c9\u30eb\u3092\u8d85\u3048\u3001\u81ea\u5df1\u8ca0\u62c5\u984d\u3082\u9ad8\u984d\u306b\u306a\u308b\u3053\u3068\u304c\u3042\u308a\u307e\u3059\u3002\u6b27\u5dde\u306e\u652f\u6255\u8005\u306f\u53b3\u683c\u306a\u8cbb\u7528\u5bfe\u52b9\u679c\u306e\u57fa\u6e96\u3092\u9069\u7528\u3057\u3001\u65b0\u8208\u56fd\u3067\u306f\u30ea\u30b9\u30c8\u4fa1\u683c\u304c\u56fd\u6c11\u4e00\u4eba\u5f53\u305f\u308a\u306e\u6240\u5f97\u3092\u4e0a\u56de\u308b\u305f\u3081\u3001\u666e\u53ca\u304c\u8457\u3057\u304f\u5236\u9650\u3055\u308c\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u65e2\u5b58\u306e\u75be\u60a3\u4fee\u98fe\u85ac\u306e\u9650\u5b9a\u7684\u306a\u6709\u52b9\u6027: \u30ea\u30eb\u30be\u30fc\u30eb\u3068\u30a8\u30c0\u30e9\u30dc\u30f3\u3068\u3044\u3063\u305f\u65e2\u5b58\u85ac\u306f\u3001\u751f\u5b58\u671f\u9593\u30922\uff5e3\u30f6\u6708\u5ef6\u9577\u3059\u308b\u306b\u904e\u304e\u305a\u3001\u6a5f\u80fd\u7684\u5229\u76ca\u3082\u907a\u4f1d\u5b50\u578b\u306b\u3088\u3063\u3066\u5927\u304d\u304f\u7570\u306a\u308a\u307e\u3059\u3002<br \/>\n*   \u30d0\u30a4\u30aa\u533b\u85ac\u54c1\/\u81ea\u5df1\u7d30\u80deCMC\u88fd\u9020\u80fd\u529b\u306e\u30dc\u30c8\u30eb\u30cd\u30c3\u30af: \u7279\u306b\u5c02\u9580\u7684\u306a\u88fd\u9020\u306b\u304a\u3044\u3066\u3001\u4f9b\u7d66\u5236\u7d04\u304c\u5e02\u5834\u306e\u6210\u9577\u3092\u59a8\u3052\u308b\u53ef\u80fd\u6027\u304c\u3042\u308a\u307e\u3059\u3002<br \/>\n*   \u30a8\u30c0\u30e9\u30dc\u30f3\u9577\u671f\u4f7f\u7528\u306b\u304a\u3051\u308b\u65b0\u305f\u306a\u5b89\u5168\u6027\u30b7\u30b0\u30ca\u30eb: \u9577\u671f\u7684\u306a\u809d\u81d3\u30a4\u30d9\u30f3\u30c8\u306b\u95a2\u3059\u308b\u5b89\u5168\u6027\u76e3\u8996\u304c\u5f37\u5316\u3055\u308c\u3066\u304a\u308a\u3001\u4e00\u90e8\u306e\u652f\u6255\u8005\u306f\u6cbb\u7642\u671f\u9593\u3092\u5236\u9650\u3059\u308b\u52d5\u304d\u3092\u898b\u305b\u3066\u3044\u307e\u3059\u3002<\/p>\n<p> \u30bb\u30b0\u30e1\u30f3\u30c8\u5206\u6790<\/p>\n<p>*   \u6cbb\u7642\u30bf\u30a4\u30d7\u5225: \u85ac\u5264\u304c\u4f9d\u7136\u3068\u3057\u3066\u53ce\u76ca\u306e\u5927\u90e8\u5206\u3092\u5360\u3081\u3066\u3044\u307e\u3059\u304c\u3001\u907a\u4f1d\u5b50\u30fbASO\u7642\u6cd5\u306f\u6025\u901f\u306b\u6210\u9577\u3057\u3066\u304a\u308a\u30012030\u5e74\u307e\u3067\u306b\u305d\u306e\u5dee\u3092\u7e2e\u3081\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u5e79\u7d30\u80de\u7642\u6cd5\u306f\u3001\u97d3\u56fd\u306eNeuronata-R\u306e\u627f\u8a8d\u3084BrainStorm\u306eNurOwn\u306e\u9032\u5c55\u306b\u3088\u308a\u3001\u30cb\u30c3\u30c1\u306a\u5e02\u5834\u3092\u5f62\u6210\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u85ac\u5264\u30af\u30e9\u30b9\u5225: \u30ea\u30eb\u30be\u30fc\u30eb\u306f\u30b8\u30a7\u30cd\u30ea\u30c3\u30af\u533b\u85ac\u54c1\u306e\u666e\u53ca\u3068\u795e\u7d4c\u79d1\u533b\u306e\u8a8d\u77e5\u5ea6\u306b\u3088\u308a\u9ad8\u3044\u30b7\u30a7\u30a2\u3092\u7dad\u6301\u3057\u3066\u3044\u307e\u3059\u304c\u3001\u8a3a\u65ad\u6642\u306e\u907a\u4f1d\u5b50\u691c\u67fb\u306e\u666e\u53ca\u306b\u4f34\u3044ASO\u304c\u6210\u9577\u3057\u3066\u3044\u307e\u3059\u3002\u30a8\u30c0\u30e9\u30dc\u30f3\u306f\u9759\u8108\u5185\u6295\u4e0e\u306e\u30b7\u30a7\u30a2\u3092\u4fdd\u6301\u3057\u3066\u3044\u307e\u3059\u304c\u3001\u9577\u671f\u7684\u306a\u809d\u81d3\u30a4\u30d9\u30f3\u30c8\u306b\u95a2\u3059\u308b\u5b89\u5168\u6027\u76e3\u8996\u306b\u76f4\u9762\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u6295\u4e0e\u7d4c\u8def\u5225: \u7d4c\u53e3\u7642\u6cd5\u304c\u5229\u4fbf\u6027\u3068\u78ba\u7acb\u3055\u308c\u305f\u511f\u9084\u30b3\u30fc\u30c9\u306b\u3088\u308a2024\u5e74\u306e\u53ce\u76ca\u306e48.2%\u3092\u5360\u3081\u307e\u3057\u305f\u3002\u9ac4\u8154\u5185\u6295\u4e0e\u306f\u3001\u75c5\u9662\u306e\u8a2d\u5099\u6295\u8cc7\u3068\u5c02\u9580\u770b\u8b77\u5e2b\u306e\u80b2\u6210\u306b\u3088\u308a\u30015.8%\u306eCAGR\u3067\u6700\u3082\u6025\u901f\u306b\u5897\u52a0\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u30a8\u30f3\u30c9\u30e6\u30fc\u30b6\u30fc\u5225: \u75c5\u9662\u306f\u8907\u96d1\u306a\u6295\u4e0e\u3068\u30e2\u30cb\u30bf\u30ea\u30f3\u30b0\u8981\u4ef6\u306b\u5bfe\u5fdc\u3067\u304d\u308b\u305f\u3081\u30012024\u5e74\u306e\u58f2\u4e0a\u306e64.3%\u3092\u5360\u3081\u307e\u3057\u305f\u3002\u3057\u304b\u3057\u3001\u5c02\u9580ALS\u30af\u30ea\u30cb\u30c3\u30af\u306f\u3001\u591a\u5206\u91ce\u9023\u643a\u30b1\u30a2\u304c\u751f\u5b58\u671f\u9593\u3092\u7d04300\u65e5\u5ef6\u9577\u3057\u3001\u5165\u9662\u3092\u534a\u6e1b\u3055\u305b\u308b\u3068\u3044\u3046\u30a8\u30d3\u30c7\u30f3\u30b9\u306b\u3088\u308a\u3001\u5e74\u95934.4%\u3067\u62e1\u5927\u3057\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u6d41\u901a\u30c1\u30e3\u30cd\u30eb\u5225: \u75c5\u9662\u85ac\u5c40\u304c2024\u5e74\u306b57.6%\u306e\u5e02\u5834\u30b7\u30a7\u30a2\u3092\u5360\u3081\u307e\u3057\u305f\u304c\u3001\u6162\u6027\u75be\u60a3\u60a3\u8005\u304c\u81ea\u5b85\u3078\u306e\u914d\u9001\u3084\u5b9a\u671f\u7684\u306a\u88dc\u5145\u3092\u6c42\u3081\u308b\u305f\u3081\u3001\u30aa\u30f3\u30e9\u30a4\u30f3\u30c1\u30e3\u30cd\u30eb\u306f6.3%\u306eCAGR\u3067\u62e1\u5927\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p> \u5730\u57df\u5206\u6790<\/p>\n<p>*   \u5317\u7c73: 2024\u5e74\u306b\u306f\u4e16\u754c\u306e\u53ce\u76ca\u306e42.40%\u3092\u5360\u3081\u3001ALS\u60a3\u8005\u306b\u5bfe\u3059\u308b\u30e1\u30c7\u30a3\u30b1\u30a2\u306e\u5373\u6642\u9069\u7528\u8cc7\u683c\u3084\u3001\u9769\u65b0\u7684\u306a\u6cbb\u7642\u3078\u306e\u65e9\u671f\u30a2\u30af\u30bb\u30b9\u3092\u53ef\u80fd\u306b\u3059\u308bFDA\u306e\u65e9\u671f\u627f\u8a8d\u304c\u727d\u5f15\u3057\u3066\u3044\u307e\u3059\u3002ACT for ALS\u30d7\u30ed\u30b0\u30e9\u30e0\u306a\u3069\u306e\u6cd5\u6574\u5099\u304c\u81e8\u5e8a\u8a66\u9a13\u30a4\u30f3\u30d5\u30e9\u3092\u62e1\u5145\u3057\u3001\u300cRight-To-Try\u300d\u898f\u5b9a\u304c\u30b3\u30f3\u30d1\u30c3\u30b7\u30e7\u30cd\u30fc\u30c8\u30e6\u30fc\u30b9\u306e\u5c0e\u5165\u3092\u52a0\u901f\u3055\u305b\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u6b27\u5dde: \u6210\u719f\u3057\u305f\u511f\u9084\u30cd\u30c3\u30c8\u30ef\u30fc\u30af\u3068\u30012024\u5e74\u306b\u521d\u306eASO\u3092\u627f\u8a8d\u3057\u305fEMA\u306e\u5354\u8abf\u7684\u306a\u627f\u8a8d\u7d4c\u8def\u304c\u7279\u5fb4\u3067\u3059\u3002\u3057\u304b\u3057\u3001\u56fd\u3054\u3068\u306e\u533b\u7642\u6280\u8853\u8a55\u4fa1\u306b\u3088\u308a\u3001\u4e0a\u5e02\u306b6\uff5e12\u30f6\u6708\u306e\u9045\u5ef6\u304c\u751f\u3058\u308b\u3053\u3068\u304c\u3042\u308a\u307e\u3059\u3002\u30c9\u30a4\u30c4\u3001\u30d5\u30e9\u30f3\u30b9\u3001\u82f1\u56fd\u306b\u62e0\u70b9\u3092\u7f6e\u304f\u7814\u7a76\u30b3\u30f3\u30bd\u30fc\u30b7\u30a2\u30e0\u304c\u3001\u5f37\u56fa\u306a\u81e8\u5e8a\u8a66\u9a13\u30a8\u30b3\u30b7\u30b9\u30c6\u30e0\u3092\u652f\u3048\u3066\u3044\u307e\u3059\u3002<br \/>\n*   \u30a2\u30b8\u30a2\u592a\u5e73\u6d0b: 2030\u5e74\u307e\u3067\u306b7.2%\u306e\u6700\u3082\u9ad8\u3044CAGR\u3092\u8a18\u9332\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u304a\u308a\u3001\u5927\u304d\u306a\u672a\u5145\u8db3\u30cb\u30fc\u30ba\u3068\u795e\u7d4c\u5b66\u30bb\u30f3\u30bf\u30fc\u306e\u6025\u901f\u306a\u62e1\u5927\u304c\u80cc\u666f\u306b\u3042\u308a\u307e\u3059\u3002\u65e5\u672c\u306f\u3001\u30a8\u30c0\u30e9\u30dc\u30f3\u306b\u95a2\u3059\u308b\u4ee5\u524d\u304b\u3089\u306e\u8a8d\u77e5\u5ea6\u3068\u795e\u7d4c\u5909\u6027\u75be\u60a3R&#038;D\u3078\u306e\u653f\u5e9c\u8cc7\u91d1\u6295\u5165\u306b\u3088\u308a\u3001\u5546\u696d\u7684\u306a\u5c0e\u5165\u3092\u30ea\u30fc\u30c9\u3057\u3066\u3044\u307e\u3059\u3002\u97d3\u56fd\u306f\u5e79\u7d30\u80de\u6cbb\u7642\u306b\u304a\u3051\u308b\u898f\u5236\u4e0a\u306e\u5148\u884c\u8005\u5229\u76ca\u3092\u6d3b\u304b\u3057\u3001\u5730\u57df\u9700\u8981\u5411\u3051\u306e\u88fd\u9020\u8f38\u51fa\u56fd\u3068\u3057\u3066\u306e\u5730\u4f4d\u3092\u78ba\u7acb\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p> \u7af6\u4e89\u74b0\u5883<\/p>\n<p>\u5e02\u5834\u96c6\u4e2d\u5ea6\u306f\u4e2d\u7a0b\u5ea6\u3067\u3042\u308a\u3001\u4e0a\u4f4d5\u793e\u304c2024\u5e74\u306e\u58f2\u4e0a\u306e\u7d0445%\u3092\u5360\u3081\u3066\u3044\u307e\u3059\u3002Biogen\u3068Ionis Pharmaceuticals\u306f\u3001\u691c\u8a3c\u6e08\u307f\u306e\u81e8\u5e8a\u30c7\u30fc\u30bf\u3068\u72ec\u81ea\u306e\u5316\u5b66\u30d7\u30e9\u30c3\u30c8\u30d5\u30a9\u30fc\u30e0\u306b\u3088\u308a\u3001ASO\u5206\u91ce\u3092\u5171\u540c\u3067\u30ea\u30fc\u30c9\u3057\u3066\u3044\u307e\u3059\u3002Mitsubishi Tanabe\u306f\u30a8\u30c0\u30e9\u30dc\u30f3\u3092\u901a\u3058\u3066\u9759\u8108\u5185\u6295\u4e0e\u306e\u30b7\u30a7\u30a2\u3092\u78ba\u4fdd\u3057\u3001Eisai\u306f\u7d4c\u53e3\u30ea\u30eb\u30be\u30fc\u30eb\u3068\u88dc\u52a9\u7684\u306a\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u8cc7\u7523\u306b\u3088\u308a\u56fd\u5185\u306e\u65e5\u672c\u5e02\u5834\u3067\u306e\u8db3\u5834\u3092\u7dad\u6301\u3057\u3066\u3044\u307e\u3059\u3002\u6210\u9577\u6226\u7565\u3068\u3057\u3066\u306f\u6226\u7565\u7684\u63d0\u643a\u304c\u4e3b\u6d41\u3067\u3042\u308a\u3001Eli Lilly\u306b\u3088\u308b2024\u5e74\u306eQurAlis\u306eUNC13A\u30d7\u30ed\u30b0\u30e9\u30e0\u306e4500\u4e07\u7c73\u30c9\u30eb\u3067\u306e\u8cb7\u53ce\u304c\u3001\u5927\u624b\u88fd\u85ac\u4f1a\u793e\u306b\u3088\u308b\u30ea\u30b9\u30af\u8efd\u6e1b\u3055\u308c\u305f\u8cc7\u7523\u306e\u8abf\u9054\u4f8b\u3068\u3057\u3066\u6319\u3052\u3089\u308c\u307e\u3059\u3002<\/p>\n<p>\u6280\u8853\u5c0e\u5165\u306f\u3001\u30b3\u30f3\u30d1\u30cb\u30aa\u30f3\u8a3a\u65ad\u3068\u9060\u9694\u30e2\u30cb\u30bf\u30ea\u30f3\u30b0\u306b\u96c6\u4e2d\u3057\u3066\u3044\u307e\u3059\u3002\u9ac4\u8154\u5185\u6295\u4e0e\u30b7\u30b9\u30c6\u30e0\u3092\u63d0\u4f9b\u3059\u308b\u30c7\u30d0\u30a4\u30b9\u4f01\u696d\u306f\u3001\u907a\u4f1d\u5b50\u6cbb\u7642\u958b\u767a\u4f01\u696d\u3068\u30af\u30ed\u30b9\u30e9\u30a4\u30bb\u30f3\u30b9\u5951\u7d04\u3092\u7d50\u3073\u3001\u75c5\u9662\u306e\u8cfc\u8cb7\u6c7a\u5b9a\u3092\u5408\u7406\u5316\u3059\u308b\u5782\u76f4\u7d71\u5408\u578b\u30b1\u30a2\u30d1\u30c3\u30b1\u30fc\u30b8\u3092\u69cb\u7bc9\u3057\u3066\u3044\u307e\u3059\u3002AI\u3092\u6d3b\u7528\u3057\u305f\u30b9\u30bf\u30fc\u30c8\u30a2\u30c3\u30d7\u4f01\u696d\u306f\u3001\u30af\u30e9\u30a6\u30c9\u30d9\u30fc\u30b9\u306e\u5275\u85ac\u30d7\u30e9\u30c3\u30c8\u30d5\u30a9\u30fc\u30e0\u3092\u6d3b\u7528\u3057\u3066\u591a\u6a19\u7684\u4f4e\u5206\u5b50\u3092\u7279\u5b9a\u3057\u3001\u53c2\u5165\u969c\u58c1\u3092\u4e0b\u3052\u3001\u65e2\u5b58\u4f01\u696d\u3088\u308a\u3082\u30b3\u30b9\u30c8\u69cb\u9020\u306e\u4f4e\u3044\u6311\u6226\u8005\u306e\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u3092\u80b2\u6210\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u88fd\u9020\u80fd\u529b\u306f\u4f9d\u7136\u3068\u3057\u3066\u7af6\u4e89\u4e0a\u306e\u5dee\u5225\u5316\u8981\u56e0\u3067\u3059\u3002\u81ea\u793e\u3067\u30aa\u30ea\u30b4\u30cc\u30af\u30ec\u30aa\u30c1\u30c9\u88fd\u9020\u30e9\u30a4\u30f3\u3092\u6301\u3064\u4f01\u696d\u306f\u3001\u5951\u7d04\u30d1\u30fc\u30c8\u30ca\u30fc\u306b\u4f9d\u5b58\u3059\u308b\u4f01\u696d\u3088\u308a\u3082\u8fc5\u901f\u306b\u898f\u6a21\u8981\u4ef6\u3092\u6e80\u305f\u3057\u3001\u4e0a\u5e02\u30b9\u30b1\u30b8\u30e5\u30fc\u30eb\u3092\u78ba\u4fdd\u3067\u304d\u307e\u3059\u3002\u3053\u308c\u306b\u5bfe\u5fdc\u3057\u3001\u3044\u304f\u3064\u304b\u306e\u65e2\u5b58\u4f01\u696d\u306f2025\u5e74\u304b\u30892026\u5e74\u306b\u304b\u3051\u3066cGMP\u65bd\u8a2d\u306e\u5897\u5f37\u8a08\u753b\u3092\u767a\u8868\u3057\u3066\u304a\u308a\u3001\u3053\u308c\u306b\u3088\u308a\u4e16\u754c\u306eASO\u751f\u7523\u80fd\u529b\u306f\u7d042\u500d\u306b\u306a\u308b\u898b\u8fbc\u307f\u3067\u3059\u3002<\/p>\n<p> \u4e3b\u8981\u4f01\u696d<\/p>\n<p>*   Mitsubishi Tanabe Pharma Corporation<br \/>\n*   CORESTEM, Inc<br \/>\n*   BrainStorm Cell Limited<br \/>\n*   Amylyx Pharmaceuticals Inc.<br \/>\n*   Biogen<\/p>\n<p> \u6700\u8fd1\u306e\u696d\u754c\u52d5\u5411<\/p>\n<p>*   2025\u5e741\u6708: QurAlis\u306f\u3001ALS\u5411\u3051\u5909\u7570\u7279\u7570\u7684ASO\u3067\u3042\u308bQRL-201\u306eANQUR\u8a66\u9a13\u3092\u7528\u91cf\u7bc4\u56f2\u8a2d\u5b9a\u6bb5\u968e\u306b\u9032\u3081\u3001\u7740\u5b9f\u306a\u9032\u5c55\u3092\u793a\u3057\u307e\u3057\u305f\u3002<br \/>\n*   2025\u5e741\u6708: Neuvivo\u306f\u3001NP001\u514d\u75ab\u7642\u6cd5\u304c\u751f\u5b58\u671f\u9593\u3092\u6700\u592717\u30f6\u6708\u5ef6\u9577\u3057\u3001\u80ba\u6a5f\u80fd\u3092\u7dad\u6301\u3057\u305f\u3053\u3068\u3092\u793a\u3059\u30c7\u30fc\u30bf\u3092\u767a\u8868\u3057\u3001\u305d\u306e\u5f8cFDA\u306b\u65b0\u85ac\u627f\u8a8d\u7533\u8acb\u3092\u63d0\u51fa\u3057\u307e\u3057\u305f\u3002<br \/>\n*   2024\u5e7412\u6708: 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