{"id":99167,"date":"2026-01-11T08:41:21","date_gmt":"2026-01-10T23:41:21","guid":{"rendered":"https:\/\/www.marketresearch.co.jp\/insights\/spinal-muscular-atrophy-treatment-mordor\/"},"modified":"2026-09-11T22:37:18","modified_gmt":"2026-09-11T13:37:18","slug":"spinal-muscular-atrophy-treatment-mordor","status":"publish","type":"post","link":"https:\/\/www.marketresearch.co.jp\/insights\/spinal-muscular-atrophy-treatment-mordor\/","title":{"rendered":"\u810a\u9ac4\u6027\u7b4b\u840e\u7e2e\u75c7\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u30fb\u30b7\u30a7\u30a2\u5206\u6790 &#8211; \u6210\u9577\u30c8\u30ec\u30f3\u30c9\u3068\u4e88\u6e2c (2025\u5e74\uff5e2030\u5e74)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.marketresearch.co.jp\/insights\/wp-content\/uploads\/2026\/01\/spinal-muscular-atrophy-treatment_1645508424348_players_graph_sma.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.marketresearch.co.jp\/insights\/wp-content\/uploads\/2026\/01\/spinal-muscular-atrophy-treatment-size-image-1751536387163.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \u306f\u3058\u3081\u306b<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \u8abf\u67fb\u306e\u524d\u63d0\u3068\u5e02\u5834\u306e\u5b9a\u7fa9<\/li>\n<li class=\"toc-level-2\">1.2 \u8abf\u67fb\u7bc4\u56f2<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \u8abf\u67fb\u65b9\u6cd5<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \u30a8\u30b0\u30bc\u30af\u30c6\u30a3\u30d6\u30b5\u30de\u30ea\u30fc<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \u5e02\u5834\u306e\u72b6\u6cc1<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \u5e02\u5834\u6982\u8981<\/li>\n<li class=\"toc-level-2\">4.2 \u5e02\u5834\u306e\u63a8\u9032\u8981\u56e0\n<ul>\n<li class=\"toc-level-3\">4.2.1 \u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u7fa9\u52d9\u5316\u306b\u3088\u308b\u6cbb\u7642\u53ef\u80fd\u306a\u60a3\u8005\u5c64\u306e\u62e1\u5927<\/li>\n<li class=\"toc-level-3\">4.2.2 \u9ad8\u6240\u5f97\u5e02\u5834\u306b\u304a\u3051\u308bSMN\u6a19\u7684\u907a\u4f1d\u5b50\u6cbb\u7642\u306e\u6025\u901f\u306a\u666e\u53ca<\/li>\n<li class=\"toc-level-3\">4.2.3 \u9ad8\u984d\u306a\u5e0c\u5c11\u75be\u60a3\u6cbb\u7642\u85ac\u306b\u5bfe\u3059\u308b\u4e16\u754c\u306e\u652f\u6255\u8005\u306e\u53d7\u5bb9<\/li>\n<li class=\"toc-level-3\">4.2.4 \u65e9\u671f\u6bb5\u968e\u8a66\u9a13\u306b\u5bfe\u3059\u308b\u64c1\u8b77\u56e3\u4f53\u304b\u3089\u306e\u8cc7\u91d1\u63d0\u4f9b\u306e\u5897\u52a0<\/li>\n<li class=\"toc-level-3\">4.2.5 SMN &amp; \u30df\u30aa\u30b9\u30bf\u30c1\u30f3\u3092\u6a19\u7684\u3068\u3059\u308b\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u4f75\u7528\u7642\u6cd5<\/li>\n<li class=\"toc-level-3\">4.2.6 \u5728\u5b85\u30c7\u30b8\u30bf\u30eb\u670d\u85ac\u9075\u5b88\u30d7\u30e9\u30c3\u30c8\u30d5\u30a9\u30fc\u30e0\u304c\u6162\u6027\u6295\u4e0e\u3092\u4fc3\u9032<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \u5e02\u5834\u306e\u963b\u5bb3\u8981\u56e0\n<ul>\n<li class=\"toc-level-3\">4.3.1 100\u4e07\u30c9\u30eb\u898f\u6a21\u306e\u4fa1\u683c\u3068\u4e0d\u78ba\u5b9f\u306a\u9577\u671f\u511f\u9084<\/li>\n<li class=\"toc-level-3\">4.3.2 \u9ac4\u8154\u5185\u6295\u4e0e\u306e\u8907\u96d1\u3055\u3068\u6ce8\u5165\u30bb\u30f3\u30bf\u30fc\u306e\u5bb9\u91cf\u5236\u7d04<\/li>\n<li class=\"toc-level-3\">4.3.3 \u65b0\u8208\u7d4c\u6e08\u56fd\u306b\u304a\u3051\u308b\u5c0f\u5150\u795e\u7d4c\u7b4b\u5c02\u9580\u533b\u306e\u4e0d\u8db3<\/li>\n<li class=\"toc-level-3\">4.3.4 AAV\u4f9b\u7d66\u306b\u304a\u3051\u308b\u30a6\u30a4\u30eb\u30b9\u30d9\u30af\u30bf\u30fc\u88fd\u9020\u306e\u30dc\u30c8\u30eb\u30cd\u30c3\u30af<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \u30d0\u30ea\u30e5\u30fc\/\u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u5206\u6790<\/li>\n<li class=\"toc-level-2\">4.5 \u898f\u5236\u74b0\u5883<\/li>\n<li class=\"toc-level-2\">4.6 \u6280\u8853\u7684\u5c55\u671b<\/li>\n<li class=\"toc-level-2\">4.7 \u30dd\u30fc\u30bf\u30fc\u306e5\u3064\u306e\u529b\u5206\u6790\n<ul>\n<li class=\"toc-level-3\">4.7.1 \u65b0\u898f\u53c2\u5165\u306e\u8105\u5a01<\/li>\n<li class=\"toc-level-3\">4.7.2 \u8cb7\u3044\u624b\/\u6d88\u8cbb\u8005\u306e\u4ea4\u6e09\u529b<\/li>\n<li class=\"toc-level-3\">4.7.3 \u4f9b\u7d66\u8005\u306e\u4ea4\u6e09\u529b<\/li>\n<li class=\"toc-level-3\">4.7.4 \u4ee3\u66ff\u54c1\u306e\u8105\u5a01<\/li>\n<li class=\"toc-level-3\">4.7.5 \u7af6\u4e89\u306e\u6fc0\u3057\u3055<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \u5e02\u5834\u898f\u6a21\u3068\u6210\u9577\u4e88\u6e2c\uff08\u91d1\u984d\uff09<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \u75be\u60a3\u30bf\u30a4\u30d7\u5225\n<ul>\n<li class=\"toc-level-3\">5.1.1 \u30bf\u30a4\u30d70<\/li>\n<li class=\"toc-level-3\">5.1.2 \u30bf\u30a4\u30d71<\/li>\n<li class=\"toc-level-3\">5.1.3 \u30bf\u30a4\u30d72<\/li>\n<li class=\"toc-level-3\">5.1.4 \u30bf\u30a4\u30d73<\/li>\n<li class=\"toc-level-3\">5.1.5 \u30bf\u30a4\u30d74<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \u6cbb\u7642\u6cd5\u5225\n<ul>\n<li class=\"toc-level-3\">5.2.1 \u907a\u4f1d\u5b50\u88dc\u5145\u7642\u6cd5<\/li>\n<li class=\"toc-level-3\">5.2.2 SMN2\u30b9\u30d7\u30e9\u30a4\u30b7\u30f3\u30b0\u4fee\u98fe\u85ac<\/li>\n<li class=\"toc-level-3\">5.2.3 \u30a2\u30f3\u30c1\u30bb\u30f3\u30b9\u30aa\u30ea\u30b4\u30cc\u30af\u30ec\u30aa\u30c1\u30c9\u7642\u6cd5<\/li>\n<li class=\"toc-level-3\">5.2.4 \u7b4b\u6a19\u7684\u7642\u6cd5 \/ \u30df\u30aa\u30b9\u30bf\u30c1\u30f3\u963b\u5bb3\u5264<\/li>\n<li class=\"toc-level-3\">5.2.5 \u652f\u6301\u7642\u6cd5\u304a\u3088\u3073\u88dc\u52a9\u7642\u6cd5<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \u6295\u4e0e\u7d4c\u8def\u5225\n<ul>\n<li class=\"toc-level-3\">5.3.1 \u7d4c\u53e3<\/li>\n<li class=\"toc-level-3\">5.3.2 \u9ac4\u8154\u5185<\/li>\n<li class=\"toc-level-3\">5.3.3 \u9759\u8108\u5185<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.4 \u5e74\u9f62\u5c64\u5225\n<ul>\n<li class=\"toc-level-3\">5.4.1 \u65b0\u751f\u5150 (0\uff5e6\u30f6\u6708)<\/li>\n<li class=\"toc-level-3\">5.4.2 \u5c0f\u5150 (6\u30f6\u6708\uff5e12\u6b73)<\/li>\n<li class=\"toc-level-3\">5.4.3 \u601d\u6625\u671f (12\uff5e18\u6b73)<\/li>\n<li class=\"toc-level-3\">5.4.4 \u6210\u4eba (18\u6b73\u4ee5\u4e0a)<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.5 \u6d41\u901a\u30c1\u30e3\u30cd\u30eb\u5225\n<ul>\n<li class=\"toc-level-3\">5.5.1 \u75c5\u9662\u85ac\u5c40<\/li>\n<li class=\"toc-level-3\">5.5.2 \u5c02\u9580\u30af\u30ea\u30cb\u30c3\u30af<\/li>\n<li class=\"toc-level-3\">5.5.3 \u30aa\u30f3\u30e9\u30a4\u30f3\u304a\u3088\u3073\u5c0f\u58f2\u85ac\u5c40<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.6 \u5730\u57df\u5225\n<ul>\n<li class=\"toc-level-3\">5.6.1 \u5317\u7c73<\/li>\n<li class=\"toc-level-4\">5.6.1.1 \u7c73\u56fd<\/li>\n<li class=\"toc-level-4\">5.6.1.2 \u30ab\u30ca\u30c0<\/li>\n<li class=\"toc-level-4\">5.6.1.3 \u30e1\u30ad\u30b7\u30b3<\/li>\n<li class=\"toc-level-3\">5.6.2 \u6b27\u5dde<\/li>\n<li class=\"toc-level-4\">5.6.2.1 \u30c9\u30a4\u30c4<\/li>\n<li class=\"toc-level-4\">5.6.2.2 \u82f1\u56fd<\/li>\n<li class=\"toc-level-4\">5.6.2.3 \u30d5\u30e9\u30f3\u30b9<\/li>\n<li class=\"toc-level-4\">5.6.2.4 \u30a4\u30bf\u30ea\u30a2<\/li>\n<li class=\"toc-level-4\">5.6.2.5 \u30b9\u30da\u30a4\u30f3<\/li>\n<li class=\"toc-level-4\">5.6.2.6 \u305d\u306e\u4ed6\u306e\u6b27\u5dde<\/li>\n<li class=\"toc-level-3\">5.6.3 \u30a2\u30b8\u30a2\u592a\u5e73\u6d0b<\/li>\n<li class=\"toc-level-4\">5.6.3.1 \u4e2d\u56fd<\/li>\n<li class=\"toc-level-4\">5.6.3.2 \u65e5\u672c<\/li>\n<li class=\"toc-level-4\">5.6.3.3 \u30a4\u30f3\u30c9<\/li>\n<li class=\"toc-level-4\">5.6.3.4 \u30aa\u30fc\u30b9\u30c8\u30e9\u30ea\u30a2<\/li>\n<li class=\"toc-level-4\">5.6.3.5 \u97d3\u56fd<\/li>\n<li class=\"toc-level-4\">5.6.3.6 \u305d\u306e\u4ed6\u306e\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b<\/li>\n<li class=\"toc-level-3\">5.6.4 \u4e2d\u6771\u304a\u3088\u3073\u30a2\u30d5\u30ea\u30ab<\/li>\n<li class=\"toc-level-4\">5.6.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.6.4.2 \u5357\u30a2\u30d5\u30ea\u30ab<\/li>\n<li class=\"toc-level-4\">5.6.4.3 \u305d\u306e\u4ed6\u306e\u4e2d\u6771\u304a\u3088\u3073\u30a2\u30d5\u30ea\u30ab<\/li>\n<li class=\"toc-level-3\">5.6.5 \u5357\u7c73<\/li>\n<li class=\"toc-level-4\">5.6.5.1 \u30d6\u30e9\u30b8\u30eb<\/li>\n<li class=\"toc-level-4\">5.6.5.2 \u30a2\u30eb\u30bc\u30f3\u30c1\u30f3<\/li>\n<li class=\"toc-level-4\">5.6.5.3 \u305d\u306e\u4ed6\u306e\u5357\u7c73<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \u7af6\u5408\u60c5\u52e2<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \u5e02\u5834\u96c6\u4e2d\u5ea6<\/li>\n<li class=\"toc-level-2\">6.2 \u5e02\u5834\u30b7\u30a7\u30a2\u5206\u6790<\/li>\n<li class=\"toc-level-2\">6.3 \u4f01\u696d\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb (\u30b0\u30ed\u30fc\u30d0\u30eb\u30ec\u30d9\u30eb\u306e\u6982\u8981\u3001\u5e02\u5834\u30ec\u30d9\u30eb\u306e\u6982\u8981\u3001\u4e3b\u8981\u30bb\u30b0\u30e1\u30f3\u30c8\u3001\u5229\u7528\u53ef\u80fd\u306a\u8ca1\u52d9\u60c5\u5831\u3001\u6226\u7565\u60c5\u5831\u3001\u4e3b\u8981\u4f01\u696d\u306e\u5e02\u5834\u30e9\u30f3\u30ad\u30f3\u30b0\/\u30b7\u30a7\u30a2\u3001\u88fd\u54c1\u30fb\u30b5\u30fc\u30d3\u30b9\u3001\u304a\u3088\u3073\u6700\u8fd1\u306e\u52d5\u5411\u3092\u542b\u3080)\n<ul>\n<li class=\"toc-level-3\">6.3.1 Biogen Inc.<\/li>\n<li class=\"toc-level-3\">6.3.2 Roche Holding AG (Genentech)<\/li>\n<li class=\"toc-level-3\">6.3.3 Novartis International AG<\/li>\n<li class=\"toc-level-3\">6.3.4 Ionis Pharmaceuticals Inc.<\/li>\n<li class=\"toc-level-3\">6.3.5 PTC Therapeutics Inc.<\/li>\n<li class=\"toc-level-3\">6.3.6 Scholar Rock Inc.<\/li>\n<li class=\"toc-level-3\">6.3.7 Cytokinetics Inc.<\/li>\n<li class=\"toc-level-3\">6.3.8 Sarepta Therapeutics Inc.<\/li>\n<li class=\"toc-level-3\">6.3.9 NMD Pharma A\/S<\/li>\n<li class=\"toc-level-3\">6.3.10 Astellas Pharma Inc.<\/li>\n<li class=\"toc-level-3\">6.3.11 Pfizer Inc.<\/li>\n<li class=\"toc-level-3\">6.3.12 Chugai Pharmaceutical Co., Ltd.<\/li>\n<li class=\"toc-level-3\">6.3.13 Sanofi S.A. (Genzyme)<\/li>\n<li class=\"toc-level-3\">6.3.14 Catalyst Pharmaceuticals<\/li>\n<li class=\"toc-level-3\">6.3.15 Regenxbio Inc.<\/li>\n<li class=\"toc-level-3\">6.3.16 Biohaven Pharmaceutical Holding Co.<\/li>\n<li class=\"toc-level-3\">6.3.17 Audentes Therapeutics (Astellas Gene Therapies)<\/li>\n<li class=\"toc-level-3\">6.3.18 BridgeBio Pharma Inc.<\/li>\n<li class=\"toc-level-3\">6.3.19 Shionogi &amp; Co., Ltd.<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \u5e02\u5834\u6a5f\u4f1a\u3068\u5c06\u6765\u5c55\u671b<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u810a\u9ac4\u6027\u7b4b\u840e\u7e2e\u75c7\uff08SMA\uff09\u6cbb\u7642\u5e02\u5834\u306e\u6982\u8981<\/p>\n<p>\u672c\u30ec\u30dd\u30fc\u30c8\u306f\u3001\u810a\u9ac4\u6027\u7b4b\u840e\u7e2e\u75c7\uff08SMA\uff09\u6cbb\u7642\u5e02\u5834\u306e\u73fe\u72b6\u3068\u5c06\u6765\u4e88\u6e2c\u306b\u3064\u3044\u3066\u8a73\u7d30\u306b\u5206\u6790\u3057\u305f\u3082\u306e\u3067\u3059\u3002\u5e02\u5834\u306f\u3001\u75be\u60a3\u30bf\u30a4\u30d7\uff08\u30bf\u30a4\u30d7I\u3001\u30bf\u30a4\u30d7II\u3001\u30bf\u30a4\u30d7III\u3001\u30bf\u30a4\u30d7IV\uff09\u3001\u6cbb\u7642\u6cd5\uff08\u907a\u4f1d\u5b50\u88dc\u5145\u7642\u6cd5\u3001\u85ac\u7269\u7642\u6cd5\uff09\u3001\u6295\u4e0e\u7d4c\u8def\uff08\u7d4c\u53e3\u3001\u9ac4\u8154\u5185\uff09\u3001\u304a\u3088\u3073\u5730\u57df\uff08\u5317\u7c73\u3001\u6b27\u5dde\u3001\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\u3001\u4e2d\u6771\u30fb\u30a2\u30d5\u30ea\u30ab\u3001\u5357\u7c73\uff09\u306b\u3088\u3063\u3066\u30bb\u30b0\u30e1\u30f3\u30c8\u5316\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u5e02\u5834\u898f\u6a21\u3068\u6210\u9577\u4e88\u6e2c<\/p>\n<p>SMA\u6cbb\u7642\u5e02\u5834\u306f\u30012025\u5e74\u306b\u306f51.7\u5104\u7c73\u30c9\u30eb\u3068\u63a8\u5b9a\u3055\u308c\u3066\u304a\u308a\u30012030\u5e74\u307e\u3067\u306b116.8\u5104\u7c73\u30c9\u30eb\u306b\u9054\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u3053\u306e\u671f\u9593\u306b\u304a\u3051\u308b\u5e74\u5e73\u5747\u6210\u9577\u7387\uff08CAGR\uff09\u306f17.68%\u3068\u975e\u5e38\u306b\u9ad8\u3044\u6210\u9577\u304c\u898b\u8fbc\u307e\u308c\u3066\u3044\u307e\u3059\u3002\u5730\u57df\u5225\u3067\u306f\u3001\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\u5730\u57df\u304c\u6700\u3082\u6025\u901f\u306b\u6210\u9577\u3059\u308b\u5e02\u5834\u3067\u3042\u308a\u3001\u5317\u7c73\u304c\u6700\u5927\u306e\u5e02\u5834\u3068\u306a\u3063\u3066\u3044\u307e\u3059\u3002\u5e02\u5834\u306e\u96c6\u4e2d\u5ea6\u306f\u4e2d\u7a0b\u5ea6\u3067\u3059\u3002<\/p>\n<p>\u4e3b\u8981\u306a\u5e02\u5834\u52d5\u5411\u3068\u6d1e\u5bdf<\/p>\n<p>\u5e02\u5834\u3092\u727d\u5f15\u3059\u308b\u8981\u56e0\uff1a<br \/>\n*   \u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u7fa9\u52d9\u5316\u306b\u3088\u308b\u6cbb\u7642\u5bfe\u8c61\u60a3\u8005\u30d7\u30fc\u30eb\u306e\u62e1\u5927\uff08CAGR\u3078\u306e\u5f71\u97ff\uff1a+3.2%\uff09: 2024\u5e741\u6708\u4ee5\u964d\u3001\u7c73\u56fd\u5168\u5dde\u3067SMA\u306e\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u304c\u7fa9\u52d9\u5316\u3055\u308c\u3001\u75c7\u72b6\u767a\u73fe\u524d\u306e\u65e9\u671f\u8a3a\u65ad\u304c\u53ef\u80fd\u306b\u306a\u308a\u307e\u3057\u305f\u3002\u3053\u308c\u306b\u3088\u308a\u3001\u6700\u9069\u306a\u30bf\u30a4\u30df\u30f3\u30b0\u3067\u306e\u9ad8\u52b9\u679c\u6cbb\u7642\u306e\u958b\u59cb\u304c\u4fc3\u9032\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u53f0\u6e7e\u3001\u30cf\u30f3\u30ac\u30ea\u30fc\u3001\u30a4\u30bf\u30ea\u30a2\u3001\u30aa\u30fc\u30b9\u30c8\u30e9\u30ea\u30a2\u3001\u30c9\u30a4\u30c4\u306a\u3069\u3067\u3082\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u304c\u5c0e\u5165\u3055\u308c\u3066\u304a\u308a\u3001\u65e9\u671f\u8a3a\u65ad\u3068\u6cbb\u7642\u958b\u59cb\u304c\u5e02\u5834\u6210\u9577\u3092\u5f37\u529b\u306b\u5f8c\u62bc\u3057\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>*   \u65b0\u898f\u6cbb\u7642\u85ac\u306e\u627f\u8a8d\u3068\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u306e\u5145\u5b9f\uff08CAGR\u3078\u306e\u5f71\u97ff\uff1a+2.8%\uff09: 2023\u5e74\u306b\u306f\u3001\u7d4c\u53e3\u85ac\u3067\u3042\u308b\u30a8\u30d6\u30ea\u30b9\u30c7\u30a3\uff08\u30ed\u30b7\u30e5\uff09\u304c\u4e73\u5150\u671f\u767a\u75c7\u578bSMA\u306e\u6cbb\u7642\u85ac\u3068\u3057\u3066\u627f\u8a8d\u3055\u308c\u3001\u5229\u4fbf\u6027\u306e\u9ad8\u3044\u6cbb\u7642\u9078\u629e\u80a2\u3092\u63d0\u4f9b\u3057\u3066\u3044\u307e\u3059\u3002\u307e\u305f\u3001\u907a\u4f1d\u5b50\u6cbb\u7642\u85ac\u30be\u30eb\u30b2\u30f3\u30b9\u30de\uff08\u30ce\u30d0\u30eb\u30c6\u30a3\u30b9\uff09\u306f\u3001\u5358\u56de\u6295\u4e0e\u3067\u52b9\u679c\u304c\u671f\u5f85\u3067\u304d\u308b\u753b\u671f\u7684\u306a\u6cbb\u7642\u6cd5\u3068\u3057\u3066\u5e02\u5834\u306b\u5927\u304d\u306a\u5f71\u97ff\u3092\u4e0e\u3048\u3066\u3044\u307e\u3059\u3002\u3055\u3089\u306b\u3001\u8907\u6570\u306e\u65b0\u898f\u6cbb\u7642\u85ac\u304c\u81e8\u5e8a\u8a66\u9a13\u6bb5\u968e\u306b\u3042\u308a\u3001\u5c06\u6765\u7684\u306a\u5e02\u5834\u62e1\u5927\u304c\u671f\u5f85\u3055\u308c\u307e\u3059\u3002<\/p>\n<p>*   \u60a3\u8005\u652f\u63f4\u30d7\u30ed\u30b0\u30e9\u30e0\u3068\u30a2\u30af\u30bb\u30b9\u6539\u5584\uff08CAGR\u3078\u306e\u5f71\u97ff\uff1a+1.5%\uff09: \u88fd\u85ac\u4f01\u696d\u3084\u60a3\u8005\u56e3\u4f53\u306b\u3088\u308b\u652f\u63f4\u30d7\u30ed\u30b0\u30e9\u30e0\u304c\u5145\u5b9f\u3057\u3066\u304a\u308a\u3001\u6cbb\u7642\u3078\u306e\u30a2\u30af\u30bb\u30b9\u304c\u6539\u5584\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u3053\u308c\u306b\u3088\u308a\u3001\u9ad8\u984d\u306a\u6cbb\u7642\u8cbb\u304c\u969c\u58c1\u3068\u306a\u3063\u3066\u3044\u305f\u60a3\u8005\u5c64\u306b\u3082\u6cbb\u7642\u304c\u5c4a\u304d\u3084\u3059\u304f\u306a\u3063\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u5e02\u5834\u3092\u963b\u5bb3\u3059\u308b\u8981\u56e0\uff1a<br \/>\n*   \u9ad8\u984d\u306a\u6cbb\u7642\u8cbb\u3068\u511f\u9084\u554f\u984c\uff08CAGR\u3078\u306e\u5f71\u97ff\uff1a-1.0%\uff09: SMA\u6cbb\u7642\u85ac\u306f\u975e\u5e38\u306b\u9ad8\u984d\u3067\u3042\u308a\u3001\u7279\u306b\u907a\u4f1d\u5b50\u6cbb\u7642\u85ac\u306f\u6570\u5104\u5186\u306b\u9054\u3057\u307e\u3059\u3002\u3053\u308c\u306b\u3088\u308a\u3001\u533b\u7642\u30b7\u30b9\u30c6\u30e0\u3078\u306e\u8ca1\u653f\u7684\u8ca0\u62c5\u304c\u5927\u304d\u304f\u3001\u4e00\u90e8\u306e\u5730\u57df\u3067\u306f\u511f\u9084\u304c\u9650\u5b9a\u7684\u3067\u3042\u308b\u305f\u3081\u3001\u6cbb\u7642\u3078\u306e\u30a2\u30af\u30bb\u30b9\u304c\u5236\u9650\u3055\u308c\u308b\u53ef\u80fd\u6027\u304c\u3042\u308a\u307e\u3059\u3002<\/p>\n<p>*   \u6cbb\u7642\u306e\u526f\u4f5c\u7528\u3068\u5b89\u5168\u6027\u3078\u306e\u61f8\u5ff5\uff08CAGR\u3078\u306e\u5f71\u97ff\uff1a-0.5%\uff09: \u907a\u4f1d\u5b50\u6cbb\u7642\u3084\u4e00\u90e8\u306e\u85ac\u7269\u7642\u6cd5\u306b\u306f\u3001\u809d\u6a5f\u80fd\u969c\u5bb3\u306a\u3069\u306e\u91cd\u7be4\u306a\u526f\u4f5c\u7528\u306e\u30ea\u30b9\u30af\u304c\u4f34\u3044\u307e\u3059\u3002\u3053\u308c\u306b\u3088\u308a\u3001\u60a3\u8005\u3084\u533b\u7642\u5f93\u4e8b\u8005\u304c\u6cbb\u7642\u9078\u629e\u306b\u614e\u91cd\u306b\u306a\u308b\u30b1\u30fc\u30b9\u304c\u3042\u308a\u3001\u5e02\u5834\u6210\u9577\u306e\u8db3\u304b\u305b\u3068\u306a\u308b\u53ef\u80fd\u6027\u304c\u3042\u308a\u307e\u3059\u3002<\/p>\n<p>\u30bb\u30b0\u30e1\u30f3\u30c8\u5225\u5206\u6790<\/p>\n<p>\u75be\u60a3\u30bf\u30a4\u30d7\u5225\uff1a<br \/>\n\u30bf\u30a4\u30d7I\u578bSMA\u304c\u5e02\u5834\u3092\u30ea\u30fc\u30c9\u3057\u3066\u304a\u308a\u3001\u3053\u308c\u306f\u6700\u3082\u91cd\u75c7\u5ea6\u304c\u9ad8\u304f\u3001\u65e9\u671f\u306b\u8a3a\u65ad\u3055\u308c\u308b\u305f\u3081\u3001\u6cbb\u7642\u4ecb\u5165\u306e\u5fc5\u8981\u6027\u304c\u9ad8\u3044\u3053\u3068\u306b\u8d77\u56e0\u3057\u307e\u3059\u3002\u3057\u304b\u3057\u3001\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u306e\u666e\u53ca\u306b\u3088\u308a\u3001\u75c7\u72b6\u767a\u73fe\u524d\u306e\u30bf\u30a4\u30d7II\u578b\u3084\u30bf\u30a4\u30d7III\u578b\u60a3\u8005\u306e\u8a3a\u65ad\u304c\u5897\u52a0\u3057\u3001\u3053\u308c\u3089\u306e\u30bb\u30b0\u30e1\u30f3\u30c8\u306e\u6210\u9577\u3082\u52a0\u901f\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u307e\u3059\u3002<\/p>\n<p>\u6cbb\u7642\u6cd5\u5225\uff1a<br \/>\n\u907a\u4f1d\u5b50\u88dc\u5145\u7642\u6cd5\u304c\u6700\u3082\u9ad8\u3044\u6210\u9577\u7387\u3092\u793a\u3059\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u3053\u308c\u306f\u3001\u5358\u56de\u6295\u4e0e\u3067\u9577\u671f\u7684\u306a\u52b9\u679c\u304c\u671f\u5f85\u3067\u304d\u308b\u30be\u30eb\u30b2\u30f3\u30b9\u30de\u306e\u3088\u3046\u306a\u753b\u671f\u7684\u306a\u6cbb\u7642\u85ac\u306e\u767b\u5834\u306b\u3088\u308b\u3082\u306e\u3067\u3059\u3002\u85ac\u7269\u7642\u6cd5\u3082\u3001\u7d4c\u53e3\u85ac\u30a8\u30d6\u30ea\u30b9\u30c7\u30a3\u306e\u3088\u3046\u306a\u5229\u4fbf\u6027\u306e\u9ad8\u3044\u9078\u629e\u80a2\u304c\u5897\u3048\u308b\u3053\u3068\u3067\u3001\u5b89\u5b9a\u3057\u305f\u6210\u9577\u3092\u7d9a\u3051\u308b\u3067\u3057\u3087\u3046\u3002<\/p>\n<p>\u6295\u4e0e\u7d4c\u8def\u5225\uff1a<br \/>\n\u9ac4\u8154\u5185\u6295\u4e0e\u304c\u73fe\u5728\u306e\u4e3b\u6d41\u3067\u3059\u304c\u3001\u7d4c\u53e3\u6295\u4e0e\u306e\u5229\u4fbf\u6027\u304b\u3089\u3001\u7d4c\u53e3\u85ac\u306e\u5e02\u5834\u30b7\u30a7\u30a2\u304c\u62e1\u5927\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u307e\u3059\u3002<\/p>\n<p>\u5730\u57df\u5225\u5206\u6790<\/p>\n<p>\u5317\u7c73\uff1a<br \/>\n\u6700\u5927\u306e\u5e02\u5834\u3067\u3042\u308a\u3001\u9ad8\u5ea6\u306a\u533b\u7642\u30a4\u30f3\u30d5\u30e9\u3001\u7a4d\u6975\u7684\u306a\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u3001\u624b\u539a\u3044\u511f\u9084\u5236\u5ea6\u304c\u5e02\u5834\u6210\u9577\u3092\u727d\u5f15\u3057\u3066\u3044\u307e\u3059\u3002\u4e3b\u8981\u306a\u88fd\u85ac\u4f01\u696d\u306e\u672c\u793e\u304c\u591a\u304f\u3001\u7814\u7a76\u958b\u767a\u3082\u6d3b\u767a\u3067\u3059\u3002<\/p>\n<p>\u6b27\u5dde\uff1a<br \/>\n\u5317\u7c73\u306b\u6b21\u3050\u5e02\u5834\u898f\u6a21\u3092\u6301\u3061\u3001\u5404\u56fd\u3067\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u306e\u5c0e\u5165\u304c\u9032\u3093\u3067\u3044\u307e\u3059\u3002\u3057\u304b\u3057\u3001\u56fd\u306b\u3088\u3063\u3066\u511f\u9084\u5236\u5ea6\u3084\u6cbb\u7642\u3078\u306e\u30a2\u30af\u30bb\u30b9\u306b\u3070\u3089\u3064\u304d\u304c\u3042\u308b\u305f\u3081\u3001\u6210\u9577\u7387\u306f\u5317\u7c73\u3088\u308a\u3084\u3084\u7de9\u3084\u304b\u3067\u3059\u3002<\/p>\n<p>\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\uff1a<br \/>\n\u6700\u3082\u6025\u901f\u306b\u6210\u9577\u3059\u308b\u5e02\u5834\u3067\u3042\u308a\u3001\u4e2d\u56fd\u3001\u30a4\u30f3\u30c9\u3001\u65e5\u672c\u306a\u3069\u306e\u4e3b\u8981\u56fd\u3067SMA\u306e\u8a8d\u77e5\u5ea6\u5411\u4e0a\u3068\u533b\u7642\u30a4\u30f3\u30d5\u30e9\u306e\u6574\u5099\u304c\u9032\u3093\u3067\u3044\u307e\u3059\u3002\u7279\u306b\u4e2d\u56fd\u3067\u306f\u3001\u5927\u898f\u6a21\u306a\u60a3\u8005\u4eba\u53e3\u3068\u653f\u5e9c\u306b\u3088\u308b\u533b\u7642\u6295\u8cc7\u306e\u5897\u52a0\u304c\u5e02\u5834\u62e1\u5927\u3092\u5f8c\u62bc\u3057\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u4e2d\u6771\u30fb\u30a2\u30d5\u30ea\u30ab\u3001\u5357\u7c73\uff1a<br \/>\n\u3053\u308c\u3089\u306e\u5730\u57df\u3067\u306f\u3001\u533b\u7642\u30a4\u30f3\u30d5\u30e9\u306e\u672a\u767a\u9054\u3084\u9ad8\u984d\u306a\u6cbb\u7642\u8cbb\u304c\u8ab2\u984c\u3068\u306a\u3063\u3066\u3044\u307e\u3059\u304c\u3001\u653f\u5e9c\u306e\u533b\u7642\u652f\u51fa\u306e\u5897\u52a0\u3084\u56fd\u969b\u7684\u306a\u652f\u63f4\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u3088\u308a\u3001\u5f90\u3005\u306b\u5e02\u5834\u304c\u62e1\u5927\u3057\u3066\u3044\u304f\u3068\u4e88\u6e2c\u3055\u308c\u307e\u3059\u3002<\/p>\n<p>\u7af6\u4e89\u74b0\u5883<\/p>\n<p>SMA\u6cbb\u7642\u5e02\u5834\u306f\u3001\u30ce\u30d0\u30eb\u30c6\u30a3\u30b9\u3001\u30ed\u30b7\u30e5\u3001\u30d0\u30a4\u30aa\u30b8\u30a7\u30f3\u306a\u3069\u306e\u5927\u624b\u88fd\u85ac\u4f01\u696d\u304c\u4e3b\u8981\u306a\u30d7\u30ec\u30a4\u30e4\u30fc\u3068\u3057\u3066\u5b58\u5728\u3057\u3001\u4e2d\u7a0b\u5ea6\u306e\u96c6\u4e2d\u5ea6\u3092\u793a\u3057\u3066\u3044\u307e\u3059\u3002\u3053\u308c\u3089\u306e\u4f01\u696d\u306f\u3001\u9769\u65b0\u7684\u306a\u6cbb\u7642\u85ac\u306e\u958b\u767a\u3001\u5e83\u7bc4\u306a\u8ca9\u58f2\u30cd\u30c3\u30c8\u30ef\u30fc\u30af\u3001\u60a3\u8005\u652f\u63f4\u30d7\u30ed\u30b0\u30e9\u30e0\u3092\u901a\u3058\u3066\u5e02\u5834\u3067\u306e\u7af6\u4e89\u512a\u4f4d\u6027\u3092\u78ba\u7acb\u3057\u3066\u3044\u307e\u3059\u3002\u65b0\u898f\u53c2\u5165\u4f01\u696d\u3082\u3001\u7279\u5b9a\u306e\u30cb\u30c3\u30c1\u306a\u6cbb\u7642\u6cd5\u3084\u6280\u8853\u3067\u5e02\u5834\u306b\u53c2\u5165\u3057\u3088\u3046\u3068\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u4e3b\u8981\u4f01\u696d\uff1a<br \/>\n*   \u30ce\u30d0\u30eb\u30c6\u30a3\u30b9\uff08Zolgensma\uff09<br \/>\n*   \u30ed\u30b7\u30e5\uff08Evrysdi\uff09<br \/>\n*   \u30d0\u30a4\u30aa\u30b8\u30a7\u30f3\uff08Spinraza\uff09<br \/>\n*   \u30d5\u30a1\u30a4\u30b6\u30fc<br \/>\n*   \u30a2\u30b9\u30c6\u30e9\u30b9\u88fd\u85ac<br \/>\n*   \u30b5\u30ce\u30d5\u30a3<br \/>\n*   \u30b0\u30e9\u30af\u30bd\u30fb\u30b9\u30df\u30b9\u30af\u30e9\u30a4\u30f3<br \/>\n*   \u30a2\u30e0\u30b8\u30a7\u30f3<br \/>\n*   \u30a4\u30fc\u30e9\u30a4\u30ea\u30ea\u30fc<br \/>\n*   \u30b8\u30e7\u30f3\u30bd\u30f3\u30fb\u30a8\u30f3\u30c9\u30fb\u30b8\u30e7\u30f3\u30bd\u30f3<\/p>\n<p>\u3053\u308c\u3089\u306e\u4f01\u696d\u306f\u3001\u7814\u7a76\u958b\u767a\u3078\u306e\u5927\u898f\u6a21\u306a\u6295\u8cc7\u3001\u6226\u7565\u7684\u63d0\u643a\u3001M&#038;A\u3092\u901a\u3058\u3066\u3001\u5e02\u5834\u3067\u306e\u5730\u4f4d\u3092\u5f37\u5316\u3057\u3066\u3044\u307e\u3059\u3002\u7279\u306b\u3001\u907a\u4f1d\u5b50\u6cbb\u7642\u3084RNA\u6a19\u7684\u6cbb\u7642\u3068\u3044\u3063\u305f\u6700\u5148\u7aef\u6280\u8853\u306e\u958b\u767a\u7af6\u4e89\u304c\u6fc0\u5316\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u7d50\u8ad6<\/p>\n<p>SMA\u6cbb\u7642\u5e02\u5834\u306f\u3001\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u306e\u7fa9\u52d9\u5316\u3001\u65b0\u898f\u6cbb\u7642\u85ac\u306e\u627f\u8a8d\u3001\u60a3\u8005\u652f\u63f4\u30d7\u30ed\u30b0\u30e9\u30e0\u306e\u5145\u5b9f\u3068\u3044\u3063\u305f\u5f37\u529b\u306a\u63a8\u9032\u8981\u56e0\u306b\u3088\u308a\u3001\u4eca\u5f8c\u3082\u9ad8\u3044\u6210\u9577\u3092\u7d9a\u3051\u308b\u3068\u4e88\u6e2c\u3055\u308c\u307e\u3059\u3002\u9ad8\u984d\u306a\u6cbb\u7642\u8cbb\u3084\u526f\u4f5c\u7528\u3068\u3044\u3063\u305f\u8ab2\u984c\u306f\u6b8b\u308b\u3082\u306e\u306e\u3001\u6280\u8853\u9769\u65b0\u3068\u533b\u7642\u30a2\u30af\u30bb\u30b9\u306e\u6539\u5584\u306b\u3088\u308a\u3001\u3088\u308a\u591a\u304f\u306eSMA\u60a3\u8005\u304c\u52b9\u679c\u7684\u306a\u6cbb\u7642\u3092\u53d7\u3051\u3089\u308c\u308b\u3088\u3046\u306b\u306a\u308b\u3067\u3057\u3087\u3046\u3002\u7279\u306b\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\u5730\u57df\u306f\u3001\u305d\u306e\u6f5c\u5728\u7684\u306a\u5e02\u5834\u898f\u6a21\u3068\u6025\u901f\u306a\u7d4c\u6e08\u6210\u9577\u306b\u3088\u308a\u3001\u5c06\u6765\u306e\u5e02\u5834\u62e1\u5927\u306e\u9375\u3092\u63e1\u308b\u5730\u57df\u3068\u306a\u308b\u3067\u3057\u3087\u3046\u3002<\/p>\n<p>\u672c\u30ec\u30dd\u30fc\u30c8\u306f\u3001\u810a\u9ac4\u6027\u7b4b\u840e\u7e2e\u75c7\uff08SMA\uff09\u6cbb\u7642\u5e02\u5834\u306b\u95a2\u3059\u308b\u8a73\u7d30\u306a\u5206\u6790\u3092\u63d0\u4f9b\u3057\u3066\u3044\u307e\u3059\u3002SMA\u306f\u3001SMN1\u907a\u4f1d\u5b50\u306e\u4e21\u30a2\u30ec\u30eb\u5909\u7570\u306b\u3088\u3063\u3066\u5f15\u304d\u8d77\u3053\u3055\u308c\u308b\u9032\u884c\u6027\u306e\u795e\u7d4c\u7b4b\u75be\u60a3\u3067\u3042\u308a\u3001\u904b\u52d5\u30cb\u30e5\u30fc\u30ed\u30f3\u306e\u5909\u6027\u3092\u3082\u305f\u3089\u3057\u3001\u767a\u75c7\u6642\u671f\u3068\u91cd\u75c7\u5ea6\u306b\u304a\u3044\u3066\u591a\u69d8\u306a\u75c7\u72b6\u3092\u5448\u3057\u307e\u3059\u3002\u672c\u5e02\u5834\u306f\u3001\u75be\u60a3\u30bf\u30a4\u30d7\u3001\u6cbb\u7642\u6cd5\u3001\u6295\u4e0e\u7d4c\u8def\u3001\u5e74\u9f62\u5c64\u3001\u6d41\u901a\u30c1\u30e3\u30cd\u30eb\u3001\u5730\u57df\u5225\u306b\u8a73\u7d30\u306b\u30bb\u30b0\u30e1\u30f3\u30c8\u5316\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u4e16\u754c\u306eSMA\u6cbb\u7642\u5e02\u5834\u306f\u30012025\u5e74\u306e51.7\u5104\u7c73\u30c9\u30eb\u304b\u30892030\u5e74\u306b\u306f116.8\u5104\u7c73\u30c9\u30eb\u3078\u3068\u6210\u9577\u3057\u3001\u4e88\u6e2c\u671f\u9593\u4e2d\u306e\u5e74\u5e73\u5747\u6210\u9577\u7387\uff08CAGR\uff09\u306f17.68%\u306b\u9054\u3059\u308b\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u5e02\u5834\u306e\u6210\u9577\u3092\u727d\u5f15\u3059\u308b\u4e3b\u306a\u8981\u56e0\u3068\u3057\u3066\u306f\u3001\u4ee5\u4e0b\u306e\u70b9\u304c\u6319\u3052\u3089\u308c\u307e\u3059\u3002\u65b0\u751f\u5150\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u306e\u7fa9\u52d9\u5316\u306b\u3088\u308a\u3001\u6cbb\u7642\u5bfe\u8c61\u3068\u306a\u308b\u60a3\u8005\u30d7\u30fc\u30eb\u304c\u62e1\u5927\u3057\u3066\u3044\u308b\u3053\u3068\u3002\u9ad8\u6240\u5f97\u56fd\u5e02\u5834\u306b\u304a\u3051\u308bSMN\u6a19\u7684\u907a\u4f1d\u5b50\u6cbb\u7642\u85ac\u306e\u6025\u901f\u306a\u666e\u53ca\u3002\u9ad8\u4fa1\u5024\u306e\u5e0c\u5c11\u75be\u60a3\u6cbb\u7642\u85ac\u306b\u5bfe\u3059\u308b\u4e16\u754c\u306e\u652f\u6255\u3044\u6a5f\u95a2\u306e\u53d7\u5bb9\u5ea6\u5411\u4e0a\u3002\u521d\u671f\u6bb5\u968e\u306e\u6cbb\u9a13\u306b\u5bfe\u3059\u308b\u30a2\u30c9\u30dc\u30ab\u30b7\u30fc\u30b0\u30eb\u30fc\u30d7\u304b\u3089\u306e\u8cc7\u91d1\u63d0\u4f9b\u306e\u5897\u52a0\u3002SMN\u304a\u3088\u3073\u30df\u30aa\u30b9\u30bf\u30c1\u30f3\u3092\u6a19\u7684\u3068\u3059\u308b\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u306e\u4f75\u7528\u7642\u6cd5\u3002\u5728\u5b85\u30c7\u30b8\u30bf\u30eb\u670d\u85ac\u30a2\u30c9\u30d2\u30a2\u30e9\u30f3\u30b9\u30d7\u30e9\u30c3\u30c8\u30d5\u30a9\u30fc\u30e0\u304c\u6162\u6027\u6295\u4e0e\u3092\u4fc3\u9032\u3057\u3066\u3044\u308b\u3053\u3068\u306a\u3069\u304c\u6319\u3052\u3089\u308c\u307e\u3059\u3002<\/p>\n<p>\u4e00\u65b9\u3067\u3001\u5e02\u5834\u306e\u6210\u9577\u3092\u6291\u5236\u3059\u308b\u8981\u56e0\u3082\u5b58\u5728\u3057\u307e\u3059\u3002\u6570\u767e\u4e07\u30c9\u30eb\u306b\u53ca\u3076\u9ad8\u984d\u306a\u85ac\u4fa1\u3068\u3001\u9577\u671f\u7684\u306a\u511f\u9084\u306e\u4e0d\u78ba\u5b9f\u6027\u3002\u9ac4\u8154\u5185\u6295\u4e0e\u306e\u8907\u96d1\u3055\u3001\u304a\u3088\u3073\u6ce8\u5165\u30bb\u30f3\u30bf\u30fc\u306b\u304a\u3051\u308b\u30ad\u30e3\u30d1\u30b7\u30c6\u30a3\u306e\u5236\u7d04\u3002\u65b0\u8208\u7d4c\u6e08\u56fd\u306b\u304a\u3051\u308b\u5c0f\u5150\u795e\u7d4c\u7b4b\u5c02\u9580\u533b\u306e\u4e0d\u8db3\u3002AAV\uff08\u30a2\u30c7\u30ce\u968f\u4f34\u30a6\u30a4\u30eb\u30b9\uff09\u4f9b\u7d66\u306b\u304a\u3051\u308b\u30a6\u30a4\u30eb\u30b9\u30d9\u30af\u30bf\u30fc\u88fd\u9020\u306e\u30dc\u30c8\u30eb\u30cd\u30c3\u30af\u306a\u3069\u304c\u8ab2\u984c\u3068\u306a\u3063\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u672c\u30ec\u30dd\u30fc\u30c8\u3067\u306f\u3001\u5e02\u5834\u3092\u591a\u89d2\u7684\u306b\u5206\u6790\u3057\u3066\u3044\u307e\u3059\u3002\u75be\u60a3\u30bf\u30a4\u30d7\u5225\u3067\u306f\u3001\u30bf\u30a4\u30d70\u304b\u3089\u30bf\u30a4\u30d74\u307e\u3067\u306e\u5404\u578b\u306b\u5206\u985e\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u6cbb\u7642\u6cd5\u5225\u3067\u306f\u3001\u907a\u4f1d\u5b50\u88dc\u5145\u7642\u6cd5\u3001SMN2\u30b9\u30d7\u30e9\u30a4\u30b7\u30f3\u30b0\u30e2\u30c7\u30a3\u30d5\u30a1\u30a4\u30a2\u3001\u30a2\u30f3\u30c1\u30bb\u30f3\u30b9\u30aa\u30ea\u30b4\u30cc\u30af\u30ec\u30aa\u30c1\u30c9\u7642\u6cd5\u3001\u7b4b\u6307\u5411\u6027\/\u30df\u30aa\u30b9\u30bf\u30c1\u30f3\u963b\u5bb3\u5264\u3001\u652f\u6301\u7642\u6cd5\u304a\u3088\u3073\u88dc\u52a9\u7642\u6cd5\u304c\u542b\u307e\u308c\u307e\u3059\u3002\u6295\u4e0e\u7d4c\u8def\u5225\u3067\u306f\u3001\u7d4c\u53e3\u3001\u9ac4\u8154\u5185\u3001\u9759\u8108\u5185\u6295\u4e0e\u304c\u5206\u6790\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u5e74\u9f62\u5c64\u5225\u3067\u306f\u3001\u65b0\u751f\u5150\uff080-6\u30f6\u6708\uff09\u3001\u5c0f\u5150\uff086\u30f6\u6708-12\u6b73\uff09\u3001\u9752\u5e74\uff0812-18\u6b73\uff09\u3001\u6210\u4eba\uff0818\u6b73\u4ee5\u4e0a\uff09\u306b\u533a\u5206\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u6d41\u901a\u30c1\u30e3\u30cd\u30eb\u5225\u3067\u306f\u3001\u75c5\u9662\u85ac\u5c40\u3001\u5c02\u9580\u30af\u30ea\u30cb\u30c3\u30af\u3001\u30aa\u30f3\u30e9\u30a4\u30f3\u304a\u3088\u3073\u5c0f\u58f2\u85ac\u5c40\u304c\u5bfe\u8c61\u3067\u3059\u3002\u5730\u57df\u5225\u3067\u306f\u3001\u5317\u7c73\u3001\u6b27\u5dde\u3001\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\u3001\u4e2d\u6771\u30fb\u30a2\u30d5\u30ea\u30ab\u3001\u5357\u7c73\u306e\u4e3b\u8981\u5730\u57df\u304a\u3088\u3073\u305d\u306e\u4e3b\u8981\u56fd\u304c\u8a73\u7d30\u306b\u5206\u6790\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u4e3b\u8981\u306a\u5e02\u5834\u30c8\u30ec\u30f3\u30c9\u3068\u3057\u3066\u30012024\u5e74\u306b\u306fSMN2\u30b9\u30d7\u30e9\u30a4\u30b7\u30f3\u30b0\u30e2\u30c7\u30a3\u30d5\u30a1\u30a4\u30a2\u304c42.92%\u306e\u5e02\u5834\u30b7\u30a7\u30a2\u3092\u5360\u3081\u3001\u305d\u306e\u78ba\u7acb\u3055\u308c\u305f\u5b89\u5168\u6027\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u3068\u5168\u3066\u306eSMA\u30bf\u30a4\u30d7\u3078\u306e\u9069\u7528\u53ef\u80fd\u6027\u306b\u3088\u308a\u3001\u6700\u5927\u306e\u53ce\u76ca\u6e90\u3068\u306a\u3063\u3066\u3044\u307e\u3059\u3002\u5730\u57df\u5225\u3067\u306f\u3001\u30a2\u30b8\u30a2\u592a\u5e73\u6d0b\u5730\u57df\u304c\u3001\u5065\u5eb7\u4fdd\u967a\u306e\u9069\u7528\u7bc4\u56f2\u306e\u62e1\u5927\u3001\u5206\u5b50\u8a3a\u65ad\u80fd\u529b\u306e\u5411\u4e0a\u3001\u5e0c\u5c11\u75be\u60a3\u6cbb\u7642\u85ac\u306b\u5bfe\u3059\u308b\u653f\u5e9c\u306e\u30a4\u30f3\u30bb\u30f3\u30c6\u30a3\u30d6\u306b\u3088\u308a\u30012030\u5e74\u307e\u306719.35%\u306eCAGR\u3067\u6700\u3082\u6025\u901f\u306a\u6210\u9577\u3092\u793a\u3059\u3068\u4e88\u6e2c\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u4e3b\u8981\u306a\u5e02\u5834\u30d7\u30ec\u30a4\u30e4\u30fc\u3068\u3057\u3066\u306f\u3001Biogen Inc.\u3001Roche Holding AG (Genentech)\u3001Novartis International AG\u3001Ionis Pharmaceuticals Inc.\u3001PTC Therapeutics Inc.\u306a\u3069\u304c\u6319\u3052\u3089\u308c\u3001\u3053\u308c\u3089\u306e\u4f01\u696d\u306e\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u3001\u5e02\u5834\u30b7\u30a7\u30a2\u3001\u6226\u7565\u7684\u60c5\u5831\u3001\u88fd\u54c1\u30fb\u30b5\u30fc\u30d3\u30b9\u3001\u6700\u8fd1\u306e\u52d5\u5411\u304c\u8a73\u7d30\u306b\u5206\u6790\u3055\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u672c\u30ec\u30dd\u30fc\u30c8\u306f\u3001\u5e02\u5834\u306e\u6a5f\u4f1a\u3068\u5c06\u6765\u306e\u5c55\u671b\u3001\u7279\u306b\u672a\u958b\u62d3\u9818\u57df\u3084\u6e80\u305f\u3055\u308c\u3066\u3044\u306a\u3044\u30cb\u30fc\u30ba\u306e\u8a55\u4fa1\u306b\u3064\u3044\u3066\u3082\u8a00\u53ca\u3057\u3066\u304a\u308a\u3001SMA\u6cbb\u7642\u5e02\u5834\u306e\u5168\u4f53\u50cf\u3092\u6df1\u304f\u7406\u89e3\u3059\u308b\u305f\u3081\u306e\u91cd\u8981\u306a\u60c5\u5831\u3092\u63d0\u4f9b\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"aioseo_notices":[],"_links":{"self":[{"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/posts\/99167"}],"collection":[{"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/comments?post=99167"}],"version-history":[{"count":1,"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/posts\/99167\/revisions"}],"predecessor-version":[{"id":99170,"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/posts\/99167\/revisions\/99170"}],"wp:attachment":[{"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/media?parent=99167"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/categories?post=99167"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.marketresearch.co.jp\/insights\/wp-json\/wp\/v2\/tags?post=99167"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}